The GuardOne clinical trial: A first-in-human, open-label, multinational phase 1/2 study of AVR-RD-02 ex vivo lentiviral vector, autologous gene therapy for Gaucher disease

被引:0
|
作者
Jacobsen, Leslie [1 ]
Kerner, Julie A. [1 ]
Ciotti, Rachel [1 ]
Golipour, Azadeh [1 ]
Yang, Josie [1 ]
Pfeifer, Richard [1 ]
Khan, Aneal [2 ]
Mason, Chris [1 ]
机构
[1] AVROBIO, Cambridge, MA USA
[2] Univ Calgary, Calgary, AB, Canada
关键词
D O I
10.1016/j.ymgme.2020.12.112
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
106
引用
收藏
页码:S51 / S52
页数:2
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