NFL AS A POSSIBLE BIOMARKER OF TREATMENT RESPONSE IN HEREDITARY ATTR AMYLOIDOSIS: DATA FROM THE PATISIRAN APOLLO OLE STUDY

被引：0
|
作者：
Sekijima, Y. [1 ]
Polydefkis, M. [2 ]
Ticau, S. [3 ]
Erbe, D. [3 ]
McManus, A. [3 ]
Aldinc, E. [3 ]
Adams, D. [4 ]
Reilly, M. M. [5 ]
Vaishnaw, A. [3 ]
Nioi, P. [3 ]
机构：
[1] Shinshu Univ Sch Med, Dept Med Neurol & Rheumatol, Nagano, Japan
[2] Johns Hopkins Univ, Sch Med, Baltimore, MD USA
[3] Alnylam Pharmaceut, Cambridge, MA USA
[4] Univ Paris Saclay, APHP, CHU Bicetre, INSERM, Le Kremlin Bicetre, France
[5] UCL Queen Sq Inst Neurol, MRC Ctr Neuromuscular Dis, London, England
来源：
JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM | 2022年 / 27卷
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R74 [神经病学与精神病学];
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页码：S12 / S13
页数：2
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