AAV Gene Therapy in a Canine Model of MPS1 Prevents and Reverses Corneal Blindness

被引：0
|
作者：
Hirsch, Matthew [1 ,2 ]
Gilger, Brian C. [3 ]
Llanga, Telmo [1 ]
Davis, Richard [1 ]
Kurtzberg, Joanne [4 ]
Samulski, Richard J. [2 ]
Miyadera, Keiko [5 ]
机构：
[1] Univ N Carolina, Ophthalmol, Chapel Hill, NC USA
[2] Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC USA
[3] North Carolina State Univ, Raleigh, NC USA
[4] Duke Univ, Durham, NC USA
[5] Univ Penn, Philadelphia, PA 19104 USA
来源：
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE | 2017年 / 58卷 / 08期
关键词：
D O I：
暂无
中图分类号：
R77 [眼科学];
学科分类号：
100212 ;
摘要：
4480
引用
收藏
页数：3
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