Eteplirsen Approved for Duchenne Muscular Dystrophy: The FDA Faces a Difficult Choice

被引：50
|
作者：
Stein, Cy A.
机构：
来源：
MOLECULAR THERAPY | 2016年 / 24卷 / 11期
关键词：
THERAPIES;
D O I：
10.1038/mt.2016.188
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
引用
收藏
页码：1884 / 1885
页数：2
相关论文
共 50 条
  • [1] Eteplirsen approved for Duchenne muscular dystrophy
    Traynor, Kate
    [J]. AMERICAN JOURNAL OF HEALTH-SYSTEM PHARMACY, 2016, 73 (21) : 1719 - 1719
  • [2] FDA Approves Eteplirsen for Duchenne Muscular Dystrophy: The Next Chapter in the Eteplirsen Saga
    Aartsma-Rus, Annemieke
    Krieg, Arthur M.
    [J]. NUCLEIC ACID THERAPEUTICS, 2017, 27 (01) : 1 - +
  • [3] Eteplirsen in the treatment of Duchenne muscular dystrophy
    Lim, Kenji Rowel Q.
    Maruyama, Rika
    Yokota, Toshifumi
    [J]. DRUG DESIGN DEVELOPMENT AND THERAPY, 2017, 11 : 533 - 545
  • [4] Eteplirsen for the Treatment of Duchenne Muscular Dystrophy
    Mendell, Jerry R.
    Rodino-Klapac, Louise R.
    Sahenk, Zarife
    Roush, Kandice
    Bird, Loren
    Lowes, Linda P.
    Alfano, Lindsay
    Gomez, Ann Maria
    Lewis, Sarah
    Kota, Janaiah
    Malik, Vinod
    Shontz, Kim
    Walker, Christopher M.
    Flanigan, Kevin M.
    Corridore, Marco
    Kean, John R.
    Allen, Hugh D.
    Shilling, Chris
    Melia, Kathleen R.
    Sazani, Peter
    Saoud, Jay B.
    Kaye, Edward M.
    [J]. ANNALS OF NEUROLOGY, 2013, 74 (05) : 637 - 647
  • [5] FDA Approval of Eteplirsen for Muscular Dystrophy
    Nelson, Stanley F.
    Miceli, M. Carrie
    [J]. JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION, 2017, 317 (14): : 1480 - 1480
  • [6] Regarding "Eteplirsen for the treatment of Duchenne muscular dystrophy"
    Unger, Ellis F.
    Califf, Robert M.
    [J]. ANNALS OF NEUROLOGY, 2017, 81 (01) : 162 - 164
  • [7] Eteplirsen for the Treatment of Duchenne Muscular Dystrophy (DMD)
    Charleston, J. S.
    Schnell, F. J.
    Dworzak, J.
    Donoghue, C.
    Lynch, J.
    Lewis, S.
    Chen, L.
    Rodino-Klapac, L. R.
    Sahenk, Z.
    Voss, J.
    DeAlwis, U.
    Frank, D. E.
    Eliopoulos, H.
    Mendell, J. R.
    [J]. NEUROLOGY, 2017, 88
  • [8] Eteplirsen (Exondys 51) for Duchenne Muscular Dystrophy
    不详
    [J]. MEDICAL LETTER ON DRUGS AND THERAPEUTICS, 2016, 58 (1507): : 145 - 146
  • [9] FDA Approval of Eteplirsen for Muscular Dystrophy Reply
    Kesselheim, Aaron S.
    Avorn, Jerry
    [J]. JAMA-JOURNAL OF THE AMERICAN MEDICAL ASSOCIATION, 2017, 317 (14): : 1481 - 1482
  • [10] Regarding "Eteplirsen for the Treatment of Duchenne Muscular Dystrophy" Reply
    Mendell, Jerry R.
    [J]. ANNALS OF NEUROLOGY, 2017, 81 (01) : 164 - 165
12345