FDA Approves Eteplirsen for Duchenne Muscular Dystrophy: The Next Chapter in the Eteplirsen Saga

被引：253
|
作者：
Aartsma-Rus, Annemieke [1 ]
Krieg, Arthur M. [2 ]
机构：
[1] Leiden Univ, Med Ctr, Postzone S4-P,Albinusdreef 2, NL-2333 ZA Leiden, Netherlands
[2] Checkmate Pharmaceut, Cambridge, MA USA
来源：
NUCLEIC ACID THERAPEUTICS | 2017年 / 27卷 / 01期
关键词：
regulatory; oligonucleotide; splicing modulation; therapy;
D O I：
10.1089/nat.2016.0657
中图分类号：
Q5 [生物化学]; Q7 [分子生物学];
学科分类号：
071010 ; 081704 ;
摘要：
[No abstract available]
引用
收藏
页码：1 / +
页数：4
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