Antisense oligonucleotide therapy for splicing defects in OPA1-related dominant optic atrophy

被引:0
|
作者
Wissinger, B. [1 ]
Synofzik, M. [2 ]
Schols, L. [2 ]
Bonifert, T. [1 ]
机构
[1] Univ Tubingen, Ctr Ophthalmol, Tubingen, Germany
[2] Univ Tubingen, Dept Neurodegenerat Dis, Hertie Inst Clin Brain Res, Tubingen, Germany
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D O I
10.1111/j.1755-3768.2017.03173
中图分类号
R77 [眼科学];
学科分类号
100212 ;
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页数:1
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