PRC1 IS AN ESSENTIAL DEPENDENCY AND THERAPEUTIC TARGET IN SMARCB1 DEFICIENT ATYPICAL TERATOID RHABDOID TUMORS

被引:0
|
作者
Alimova, Irina [1 ,2 ]
Danis, Ettiene [1 ]
Weetall, Marla [3 ]
Pierce, Angelela M. [1 ,2 ]
Balakrishnan, Ilango [1 ]
Wang, Dong [1 ]
Foreman, Nicholas K. [1 ,2 ,4 ]
Baird, John [3 ]
Hoffman, Lindsey [1 ,2 ]
Venkataraman, Sujatha [1 ,2 ]
Vibhakar, Rajeev [1 ,2 ,4 ]
机构
[1] Univ Colorado, Dept Pediat, Anschutz Med Campus, Aurora, CO USA
[2] Childrens Hosp Colorado, Morgan Adams Fdn Pediat Brain Tumor Res Program, Aurora, CO USA
[3] PTC Therapeut Inc, South Plainfield, NJ USA
[4] Univ Colorado, Dept Neurosurg, Aurora, CO USA
关键词
D O I
10.1093/neuonc/noz036.004
中图分类号
R73 [肿瘤学];
学科分类号
100214 ;
摘要
ATRT-05
引用
收藏
页码:63 / 64
页数:2
相关论文
共 50 条
  • [41] Frizzled-1 receptor, a potential therapeutic target for atypical teratoid rhabdoid tumor
    Chakravadhanula, Madhavi
    Ozols, Victor
    Hampton, Chris
    Bhardwaj, Ratan
    CANCER RESEARCH, 2014, 74 (19)
  • [42] Spectrum of SMARCB1/INI1 Mutations in Familial and Sporadic Rhabdoid Tumors
    Eaton, Katherine W.
    Tooke, Laura S.
    Wainwright, Luanne M.
    Judkins, Alexander R.
    Biegel, Jaclyn A.
    PEDIATRIC BLOOD & CANCER, 2011, 56 (01) : 7 - 15
  • [43] SMARCB1(INI1)-deficient undifferentiated carcinoma with rhabdoid features of anorectal origin
    Dihowm, Hanan
    Amin, Manik
    Ballentine, Samuel
    CURRENT PROBLEMS IN CANCER: CASE REPORTS, 2021, 4
  • [44] SMARCB1-DEPENDENCIES IN ATYPICAL TERATOID/RHABDOID TUMOURS: A STRATEGY FOR PRE-CLINICAL THERAPEUTIC TARGET IDENTIFICATION IN THE ABSENCE OF ACTIONABLE MUTATIONS
    Finetti, Martina Anna
    Selby, Matthew P.
    Pons, Alicia del-Carpio
    Batting, Sarah
    Wood, James A.
    Barker, James M.
    Smith, Amanda
    Crosier, Stephen
    Bashton, Matthew
    Pickles, Jessica C.
    Fairchild, Amy R.
    Avery, Aimee
    O'Hare, Patricia
    Pizer, Barry
    Brennan, Bernadette
    Lowis, Stephen
    Hargrave, Darren
    Jacques, Thomas S.
    Bailey, Simon
    Clifford, Steven C.
    Williamson, Daniel
    NEURO-ONCOLOGY, 2018, 20 : 32 - 33
  • [45] Selective inhibition of the CoREST complex as a novel therapeutic target of atypical teratoid rhabdoid tumors
    Geethadevi, Anupa
    Collard, Marianne
    Findlay, Tyler
    Deng, Yiming
    Fisher, Robert
    Vaidya, Nikhil
    Eberhart, Charles
    Cole, Philip A.
    Alani, Rhoda
    Rubens, Jeffrey
    Raabe, Eric
    CANCER RESEARCH, 2024, 84 (06)
  • [46] Inhibition of nuclear export restores nuclear localization and residual tumor suppressor function of truncated SMARCB1/INI1 protein in a molecular subset of atypical teratoid/rhabdoid tumors
    Pathak, Rajiv
    Zin, Francesca
    Thomas, Christian
    Bens, Susanne
    Gayden, Tenzin
    Karamchandani, Jason
    Dudley, Roy W.
    Nemes, Karolina
    Johann, Pascal D.
    Oyen, Florian
    Kordes, Uwe
    Jabado, Nada
    Siebert, Reiner
    Paulus, Werner
    Kool, Marcel
    Fruhwald, Michael C.
    Albrecht, Steffen
    Kalpana, Ganjam V.
    Hasselblatt, Martin
    ACTA NEUROPATHOLOGICA, 2021, 142 (02) : 361 - 374
  • [47] Inhibition of nuclear export restores nuclear localization and residual tumor suppressor function of truncated SMARCB1/INI1 protein in a molecular subset of atypical teratoid/rhabdoid tumors
    Rajiv Pathak
    Francesca Zin
    Christian Thomas
    Susanne Bens
    Tenzin Gayden
    Jason Karamchandani
    Roy W. Dudley
    Karolina Nemes
    Pascal D. Johann
    Florian Oyen
    Uwe Kordes
    Nada Jabado
    Reiner Siebert
    Werner Paulus
    Marcel Kool
    Michael C. Frühwald
    Steffen Albrecht
    Ganjam V. Kalpana
    Martin Hasselblatt
    Acta Neuropathologica, 2021, 142 : 361 - 374
  • [48] Brachyury expression in intracranial SMARCB1-deficient tumors: important points for distinguishing poorly differentiated chordoma from atypical teratoid/rhabdoid tumor
    Kohashi, Kenichi
    Yamamoto, Hidetaka
    Yamada, Yuichi
    Kinoshita, Izumi
    Oda, Yoshinao
    HUMAN PATHOLOGY, 2021, 112 : 1 - 8
  • [49] Oncogenic roles of SMARCB1/INI1 and its deficient tumors
    Kohashi, Kenichi
    Oda, Yoshinao
    CANCER SCIENCE, 2017, 108 (04) : 547 - 552
  • [50] SMARCB1 Gene Therapy Using a Novel Tumor-Targeted Nanomedicine Enhances Anti-Cancer Efficacy in a Mouse Model of Atypical Teratoid Rhabdoid Tumors
    Kim, Sang-Soo
    Moghe, Manish
    Rait, Antonina
    Donaldson, Kathryn
    Harford, Joe B.
    Chang, Esther H.
    INTERNATIONAL JOURNAL OF NANOMEDICINE, 2024, 19 : 5973 - 5993