Vector Shedding and Blood Biodistribution in Patients with Severe Hemophilia a Following Administration of Valoctocogene Roxaparvovec

被引:0
|
作者
Clark, Annie
Hammon, Kevin
Sandza, Krystal
Torres, Richard
Koziol, Elli
Holcomb, Jennifer
Kim, Benjamin
Jayaram, Kala
Russell, Chris
Vettermann, Christian
Henshaw, Joshua
机构
关键词
D O I
10.1182/blood-2020-136459
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页数:3
相关论文
共 50 条
  • [31] Recombinant human factor VIIa (rFVIIa) cleared principally by antithrombin following intravenous administration in hemophilia patients
    Agerso, H.
    Brophy, D. F.
    Pelzer, H.
    Martin, E. J.
    Carr, M.
    Hedner, U.
    Ezban, M.
    JOURNAL OF THROMBOSIS AND HAEMOSTASIS, 2011, 9 (02) : 333 - 338
  • [32] THERAPEUTIC OUTCOMES FOLLOWING TOCILIZUMAB ADMINISTRATION IN PATIENTS WITH SEVERE COVID-19
    Kline, Jonathan
    Patel, Payal
    Palma, Stephanie
    Pasqualicchio, Michael
    Clarke, Heidi
    CRITICAL CARE MEDICINE, 2021, 49 (01) : 84 - 84
  • [33] The impact of antithrombin administration on organ failure in patients following severe burn injury
    Lavrentieva, A.
    Lazaridis, L.
    Parlapani, A.
    Thomareis, O.
    Giala, M.
    EUROPEAN JOURNAL OF ANAESTHESIOLOGY, 2004, 21 : 165 - 165
  • [34] BIODISTRIBUTION AND SHEDDING ANALYSIS FOLLOWING TREATMENT WITH RP1 ONCOLYTIC IMMUNOTHERAPY IN THE SKIN CANCER PATIENTS FROM THE IGNYTE CLINICAL TRIAL
    Milhem, Mohammed
    VanderWalde, Ari
    Bowles, Tawnya
    Sacco, Joseph
    Olsson-Brown, Anna
    Niu, Jiaxin
    Tsai, Katy
    Chesney, Jason
    Chmielowski, Bartosz
    Samson, Adel
    Rhodes, Terence
    In, Gino
    Pavlick, Anna
    Wise-Draper, Trisha
    Sanmamed, Miguel
    Kalbasi, Alireza
    Love, Colin
    Clack, Aaron
    Hou, Jeannie
    Bommareddy, Praveen
    Coffin, Robert
    Middleton, Mark
    Harrington, Kevin
    JOURNAL FOR IMMUNOTHERAPY OF CANCER, 2022, 10 : A643 - A643
  • [35] The safety and efficacy of recombinant human blood coagulation factor IX in previously untreated patients with severe or moderately severe hemophilia B
    Shapiro, AD
    Di Paola, J
    Cohen, A
    Pasi, KJ
    Heisel, MA
    Blanchette, VS
    Abshire, TC
    Hoots, WK
    Lusher, JM
    Negrier, C
    Rothschild, C
    Roth, DA
    BLOOD, 2005, 105 (02) : 518 - 525
  • [36] EMPIRICAL ADMINISTRATION OF CARBENICILLIN AND GENTAMICIN FOR SEVERE INFECTION IN PATIENTS WITH MALIGNANT BLOOD DISEASE
    FIERE, D
    BRYON, PA
    MARTIN, C
    REVOL, L
    SEMAINE DES HOPITAUX THERAPEUTIQUE, 1975, 51 (03): : 153 - 157
  • [37] Non-viral gene transfer of blood coagulation factor VIII in patients with severe hemophilia A.
    Roth, DA
    Tawa, NE
    O'Brien, J
    Levine, JD
    Furie, B
    Furie, BC
    Proper, J
    Roman, VA
    Sabine, ZM
    Lamsa, JC
    Gunter, KC
    Phillips, CW
    Savioli, NA
    Treco, DA
    Selden, RF
    BLOOD, 2000, 96 (11) : 590A - +
  • [38] Early Clinical Trial Results Following Administration of a Low Dose of a Novel Self Complementary Adeno-Associated Viral Vector Encoding Human Factor IX In Two Subjects with Severe Hemophilia B
    Nathwani, Amit
    Tuddenham, Edward
    Rosales, Cecilia
    McIntosh, Jenny
    Riddell, Anne
    Rustagi, Pradip
    Glader, Bertil
    Kay, Mark
    Allay, James
    Coleman, John
    Sleep, Susan
    High, Katherine A.
    Mingozzi, Federico
    Gray, John T.
    Reiss, Ulrike M.
    Nienhuis, Arthur W.
    Davidoff, Andrew
    BLOOD, 2010, 116 (21) : 114 - 114
  • [39] Experience of NovoSeven administration in the management of severe haemorrhage following cardiac surgery of nonhaemophilic patients
    G Michalska
    R Stanek
    Critical Care, 11 (Suppl 2):
  • [40] Stable Factor IX Activity Following AAV-Mediated Gene Transfer in Patients with Severe Hemophilia B
    Davidoff, Andrew
    Tuddenham, Edward G. D.
    Rangarajan, Savita
    Rosales, Cecilia
    McIntosh, Jenny
    Chowdary, Pratima
    Riddell, Anne
    Glader, Bertil
    Rustagi, Pradip
    Ng, Catherine
    Kay, Mark
    Zhou, Junfang
    Spence, Yunyu
    Morton, Christopher
    Allay, James
    Sleep, Susan
    Basner-Tschakarjan, Etiena
    Mingozzi, Federico
    High, Katherine A.
    Gray, John T.
    Reiss, Ulrike M.
    Nienhuis, Arthur W.
    Nathwani, Amit C.
    BLOOD, 2012, 120 (21)