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- [1] Valoctocogene Roxaparvovec (Roctavian) - A Gene Therapy for Severe Hemophilia AMEDICAL LETTER ON DRUGS AND THERAPEUTICS, 2023, 65 (1686): : 157 - 158不详论文数: 0 引用数: 0 h-index: 0
- [2] Comparative Effectiveness of Valoctocogene Roxaparvovec and Prophylactic Factor VIII Replacement in Severe Hemophilia AADVANCES IN THERAPY, 2024, 41 (06) : 2267 - 2281Oldenburg, Johannes论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Bonn, Inst Expt Haematol & Transfus Med, Bonn, Germany Univ Hosp Bonn, Ctr Rare Dis, Bonn, Germany Univ Hosp Bonn, Inst Expt Haematol & Transfus Med, Bonn, GermanyChambost, Herve论文数: 0 引用数: 0 h-index: 0机构: Children Hosp La Timone, AP HM, Dept Pediat Hematol Oncol, Marseille, France Aix Marseille Univ, INSERM, INRA, C2VN, Marseille, France Univ Hosp Bonn, Inst Expt Haematol & Transfus Med, Bonn, GermanyLiu, Hai论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Univ Hosp Bonn, Inst Expt Haematol & Transfus Med, Bonn, GermanyHawes, Charles论文数: 0 引用数: 0 h-index: 0机构: BioMarin UK Ltd, London, England Univ Hosp Bonn, Inst Expt Haematol & Transfus Med, Bonn, GermanyYou, Xiaojun论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Univ Hosp Bonn, Inst Expt Haematol & Transfus Med, Bonn, GermanyYang, Xinqun论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Univ Hosp Bonn, Inst Expt Haematol & Transfus Med, Bonn, GermanyNewman, Vanessa论文数: 0 引用数: 0 h-index: 0机构: BioMarin UK Ltd, London, England Univ Hosp Bonn, Inst Expt Haematol & Transfus Med, Bonn, GermanyRobinson, Tara M.论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Univ Hosp Bonn, Inst Expt Haematol & Transfus Med, Bonn, GermanyHatswell, Anthony J.论文数: 0 引用数: 0 h-index: 0机构: DeltaHat Ltd, Nottingham, England UCL, Dept Stat Sci, London, England Univ Hosp Bonn, Inst Expt Haematol & Transfus Med, Bonn, GermanyHinds, David论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Univ Hosp Bonn, Inst Expt Haematol & Transfus Med, Bonn, GermanySantos, Sandra论文数: 0 引用数: 0 h-index: 0机构: BioMarin UK Ltd, London, England Univ Hosp Bonn, Inst Expt Haematol & Transfus Med, Bonn, GermanyOzelo, Margareth论文数: 0 引用数: 0 h-index: 0机构: Univ Estadual Campinas, Sch Med Sci, Dept Internal Med, Hemoctr UNICAMP, Campinas, SP, Brazil Univ Hosp Bonn, Inst Expt Haematol & Transfus Med, Bonn, Germany
- [3] IMPACT OF VALOCTOCOGENE ROXAPARVOVEC ON THE ECONOMIC BURDEN OF ADULTS WITH SEVERE HEMOPHILIA A MANAGED WITH PROPHYLAXIS IN THE UNITED STATESVALUE IN HEALTH, 2023, 26 (12) : S190 - S190Wang, T.论文数: 0 引用数: 0 h-index: 0机构: Anal Grp Inc, Menlo Pk, CA USA Anal Grp Inc, Menlo Pk, CA USAChen, E.论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Anal Grp Inc, Menlo Pk, CA USARegan, C.论文数: 0 引用数: 0 h-index: 0机构: Anal Grp Inc, San Francisco, CA USA Anal Grp Inc, Menlo Pk, CA USACook, K.论文数: 0 引用数: 0 h-index: 0机构: Anal Grp Inc, Menlo Pk, CA USA Anal Grp Inc, Menlo Pk, CA USAKirson, N.论文数: 0 引用数: 0 h-index: 0机构: Anal Grp Inc, Boston, MA USA Anal Grp Inc, Menlo Pk, CA USASantos, S.论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, London, England Anal Grp Inc, Menlo Pk, CA USAPezalla, E.论文数: 0 引用数: 0 h-index: 0机构: Enlightenment Bioconsult LLC, Daytona Beach, FL USA Anal Grp Inc, Menlo Pk, CA USASkinner, M.论文数: 0 引用数: 0 h-index: 0机构: Inst Policy Adv Ltd, Washington, DC USA Anal Grp Inc, Menlo Pk, CA USA
- [4] Persistence of haemostatic response following gene therapy with valoctocogene roxaparvovec in severe haemophilia AHAEMOPHILIA, 2021, 27 (06) : 947 - 956Pasi, K. John论文数: 0 引用数: 0 h-index: 0机构: Barts & London Queen Marys Sch Med & Dent, London, England Barts & London Queen Marys Sch Med & Dent, London, EnglandLaffan, Michael论文数: 0 引用数: 0 h-index: 0机构: Imperial Coll London, Ctr Haematol, London, England Barts & London Queen Marys Sch Med & Dent, London, EnglandRangarajan, Savita论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Southampton, Southampton, Hants, England Barts & London Queen Marys Sch Med & Dent, London, EnglandRobinson, Tara M.论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Barts & London Queen Marys Sch Med & Dent, London, EnglandMitchell, Nina论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Barts & London Queen Marys Sch Med & Dent, London, EnglandLester, Will论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Birmingham NHS Fdn Trust, Birmingham, W Midlands, England Barts & London Queen Marys Sch Med & Dent, London, EnglandSymington, Emily论文数: 0 引用数: 0 h-index: 0机构: Cambridge Univ Hosp NHS Fdn Trust, Cambridge, England Barts & London Queen Marys Sch Med & Dent, London, EnglandMadan, Bella论文数: 0 引用数: 0 h-index: 0机构: Guys & St Thomas NHS Fdn Trust, London, England Barts & London Queen Marys Sch Med & Dent, London, EnglandYang, Xinqun论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Barts & London Queen Marys Sch Med & Dent, London, EnglandKim, Benjamin论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Barts & London Queen Marys Sch Med & Dent, London, EnglandPierce, Glenn F.论文数: 0 引用数: 0 h-index: 0机构: Barts & London Queen Marys Sch Med & Dent, London, EnglandWong, Wing Yen论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Barts & London Queen Marys Sch Med & Dent, London, England
- [5] SAFETY AND EFFICACY OF VALOCTOCOGENE ROXAPARVOVEC GENE TRANSFER FOR SEVERE HEMOPHILIA A: AN UPDATE FROM 4 YEARS AFTER TREATMENTAMERICAN JOURNAL OF HEMATOLOGY, 2024, 100 : 72 - 73Leavitt, Andrew D.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, San Francisco, CA 94143 USA Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, San Francisco, CA 94143 USA论文数: 引用数: h-index:机构:Symington, Emily论文数: 0 引用数: 0 h-index: 0机构: Cambridge Univ Hosp NHS Fdn Trust, Cambridge, England Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, San Francisco, CA 94143 USAQuon, Doris V.论文数: 0 引用数: 0 h-index: 0机构: Orthopaed Hemophilia Treatment Ctr, Los Angeles, CA USA Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, San Francisco, CA 94143 USAGiermasz, Adam论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Hemophilia Treatment Ctr, Sacramento, CA 95817 USA Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, San Francisco, CA 94143 USAKey, Nigel S.论文数: 0 引用数: 0 h-index: 0机构: Univ North Carolina, UNC Blood Res Ctr, Chapel Hill, NC 27515 USA Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, San Francisco, CA 94143 USAPipe, Steven W.论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Dept Pediat, Ann Arbor, MI 48109 USA Univ Michigan, Dept Pathol, Ann Arbor, MI 48109 USA Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, San Francisco, CA 94143 USAMadan, Bella论文数: 0 引用数: 0 h-index: 0机构: Guys & St Thomas NHS Fdn Trust, London, England Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, San Francisco, CA 94143 USAChou, Sheng-Chieh论文数: 0 引用数: 0 h-index: 0机构: Natl Taiwan Univ Hosp, Div Hematol, Dept Internal Med, Taipei, Taiwan Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, San Francisco, CA 94143 USAKlamroth, Robert论文数: 0 引用数: 0 h-index: 0机构: Vivantes Klinikum Friedrichshain, Vasc Med & Haemostaseol, Berlin, Germany Univ Bonn, Univ Hosp Bonn, Fac Med, Inst Expt Hematol & Transfus Med, Bonn, Germany Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, San Francisco, CA 94143 USAMason, Jane论文数: 0 引用数: 0 h-index: 0机构: Royal Brisbane & Womens Hosp, Queensland Hemophilia Ctr, Canc Care Serv, Brisbane, Qld, Australia Univ Queensland, Brisbane, Qld, Australia Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, San Francisco, CA 94143 USA论文数: 引用数: h-index:机构:Yu, Hua论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, San Francisco, CA 94143 USARobinson, Tara M.论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, San Francisco, CA 94143 USAOzelo, Margareth C.论文数: 0 引用数: 0 h-index: 0机构: Univ Estadual Campinas, Sch Med Sci, Dept Internal Med, Hemoctr UNICAMP, Campinas, Brazil Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, San Francisco, CA 94143 USA
- [6] Achievement of normal factor VIII activity following gene transfer with valoctocogene roxaparvovec (BMN 270): Long-term efficacy and safety results in patients with severe hemophilia AHAEMOPHILIA, 2018, 24 : 65 - 65Rangarajan, Savita论文数: 0 引用数: 0 h-index: 0机构: Basingstoke & North Hampshire Hosp NHS Fdn Trust, Basingstroke, Hants, England Basingstoke & North Hampshire Hosp NHS Fdn Trust, Basingstroke, Hants, EnglandKim, Benjamin论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Basingstoke & North Hampshire Hosp NHS Fdn Trust, Basingstroke, Hants, EnglandLester, Will论文数: 0 引用数: 0 h-index: 0机构: Queen Elizabeth Hosp Birmingham, Edgbaston, England Basingstoke & North Hampshire Hosp NHS Fdn Trust, Basingstroke, Hants, EnglandSymington, Emily论文数: 0 引用数: 0 h-index: 0机构: Addenbrookes Hosp, Dept Haematol, Cambridge, England Basingstoke & North Hampshire Hosp NHS Fdn Trust, Basingstroke, Hants, EnglandMadan, Bella论文数: 0 引用数: 0 h-index: 0机构: St Thomas Hosp, Ctr Haemostasis & Thrombosis, London, England Basingstoke & North Hampshire Hosp NHS Fdn Trust, Basingstroke, Hants, EnglandLaffan, Michael论文数: 0 引用数: 0 h-index: 0机构: Hammersmith Hosp, Haemophilia Ctr, London, England Basingstoke & North Hampshire Hosp NHS Fdn Trust, Basingstroke, Hants, EnglandTavakkoli, Fatemeh论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Basingstoke & North Hampshire Hosp NHS Fdn Trust, Basingstroke, Hants, EnglandPierce, Glenn论文数: 0 引用数: 0 h-index: 0机构: Basingstoke & North Hampshire Hosp NHS Fdn Trust, Basingstroke, Hants, EnglandWong, Wing Yen论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Basingstoke & North Hampshire Hosp NHS Fdn Trust, Basingstroke, Hants, EnglandPasi, John论文数: 0 引用数: 0 h-index: 0机构: Barts & London Queen Marys Sch Med & Dent, London, England Basingstoke & North Hampshire Hosp NHS Fdn Trust, Basingstroke, Hants, England
- [7] Health-Related Quality of Life Following Valoctocogene Roxaparvovec Gene Therapy for Severe Hemophilia A in the Phase 3 Trial GENEr8-1BLOOD, 2021, 138O'Mahony, Brian论文数: 0 引用数: 0 h-index: 0机构: Irish Haemophilia Soc, Dublin, Ireland Trinity Coll Dublin, Dublin, Ireland Irish Haemophilia Soc, Dublin, Ireland论文数: 引用数: h-index:机构:Peerlinck, Kathelijne论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Leuven, Dept Vasc Med, Leuven, Belgium Univ Hosp Leuven, Haemostasis & Haemophilia Ctr, Leuven, Belgium Irish Haemophilia Soc, Dublin, IrelandWang, Jiaan-Der论文数: 0 引用数: 0 h-index: 0机构: Taichung Vet Gen Hosp, Ctr Rare Dis & Hemophilia, Taichung, Taiwan Irish Haemophilia Soc, Dublin, IrelandLowe, Gillian论文数: 0 引用数: 0 h-index: 0机构: Queen Elizabeth Hosp, West Midlands Comprehens Care Haemophilia Ctr, Birmingham, W Midlands, England Irish Haemophilia Soc, Dublin, IrelandTan, Chee Wee论文数: 0 引用数: 0 h-index: 0机构: Royal Adelaide Hosp, Dept Haematol, Adelaide, SA, Australia Irish Haemophilia Soc, Dublin, IrelandGiermasz, Adam论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Hemophilia Treatment Ctr, Sacramento, CA 95817 USA Irish Haemophilia Soc, Dublin, IrelandTran, Huyen A.论文数: 0 引用数: 0 h-index: 0机构: Alfred Hosp, Haemophilia Treatment Ctr, Haemostasis & Thrombosis Unit, Melbourne, Vic, Australia Irish Haemophilia Soc, Dublin, IrelandKhoo, Teh-Liane论文数: 0 引用数: 0 h-index: 0机构: Royal Prince Alfred Hosp, Inst Haematol, Camperdown, NSW, Australia Irish Haemophilia Soc, Dublin, IrelandCockrell, Erin论文数: 0 引用数: 0 h-index: 0机构: St Josephs Childrens Hosp, Pediat Hematol Oncol, Tampa, FL USA Irish Haemophilia Soc, Dublin, IrelandPepperell, Dominic论文数: 0 引用数: 0 h-index: 0机构: Fiona Stanley Hosp, Dept Haematol, Murdoch, WA, Australia Irish Haemophilia Soc, Dublin, IrelandChambost, Herve论文数: 0 引用数: 0 h-index: 0机构: Aix Marseille Univ, Dept Pediat Hematol Oncol, Children Hosp La Timone, AP HM,INSERM,INRA,C2VN, Marseille, France Irish Haemophilia Soc, Dublin, IrelandLopez Fernandez, Maria Fernanda论文数: 0 引用数: 0 h-index: 0机构: Complejo Hosp Univ A Coruna, La Coruna, Spain Irish Haemophilia Soc, Dublin, IrelandKazmi, Rashid论文数: 0 引用数: 0 h-index: 0机构: Southampton Univ Hosp, Dept Haematol, Southampton, Hants, England Irish Haemophilia Soc, Dublin, IrelandMajerus, Elaine论文数: 0 引用数: 0 h-index: 0机构: Washington Univ, Dept Med, St Louis, MO USA Irish Haemophilia Soc, Dublin, Ireland论文数: 引用数: h-index:机构:Klamroth, Robert论文数: 0 引用数: 0 h-index: 0机构: Vivantes Klinikum Friedrichshain, Comprehens Care Haemophilia Treatment Ctr, Berlin, Germany Irish Haemophilia Soc, Dublin, IrelandQuinn, Jennifer论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Irish Haemophilia Soc, Dublin, IrelandYu, Hua论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Irish Haemophilia Soc, Dublin, IrelandWong, Wing Yen论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Irish Haemophilia Soc, Dublin, IrelandLawal, Adebayo论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Irish Haemophilia Soc, Dublin, IrelandRobinson, Tara M.论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Irish Haemophilia Soc, Dublin, IrelandKim, Benjamin论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Irish Haemophilia Soc, Dublin, Ireland
- [8] Health-related quality of life following valoctocogene roxaparvovec gene therapy for severe hemophilia A in the phase 3 trial GENEr8-1JOURNAL OF THROMBOSIS AND HAEMOSTASIS, 2023, 21 (12) : 3450 - 3462O'Mahony, Brian论文数: 0 引用数: 0 h-index: 0机构: Irish Haemophilia Soc, Dublin, Ireland Trinity Coll Dublin, Dublin, Ireland Irish Haemophilia Soc, Dublin, IrelandDunn, Amy L.论文数: 0 引用数: 0 h-index: 0机构: Nationwide Childrens Hosp, Div Hematol Oncol BMT, Columbus, OH USA Ohio State Univ, Coll Med, Columbus, OH USA Irish Haemophilia Soc, Dublin, IrelandLeavitt, Andrew D.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, San Francisco, CA USA Irish Haemophilia Soc, Dublin, Ireland论文数: 引用数: h-index:机构:Ozelo, Margareth C.论文数: 0 引用数: 0 h-index: 0机构: Univ Estadual Campinas, Dept Internal Med, UNICAMP, Sch Med Sci,Hemooctr, Campinas, SP, Brazil Irish Haemophilia Soc, Dublin, Ireland论文数: 引用数: h-index:机构:Peerlinck, Kathelijne论文数: 0 引用数: 0 h-index: 0机构: Haemophilia Ctr Univ Hosp, Dept Vasc Med & Haemostasis, Leuven, Belgium Univ Hosp Leuven, Haemophilia Ctr, Leuven, Belgium Irish Haemophilia Soc, Dublin, IrelandWang, Jiaan-Der论文数: 0 引用数: 0 h-index: 0机构: Taichung Vet Gen Hosp, Ctr Rare Dis & Hemophilia, Taichung, Taiwan Irish Haemophilia Soc, Dublin, IrelandLowe, Gillian C.论文数: 0 引用数: 0 h-index: 0机构: Queen Elizabeth Hosp, W Midlands Adult Comprehens Care Haemophilia Ctr, Birmingham, W Midlands, England Irish Haemophilia Soc, Dublin, IrelandTan, Chee Wee论文数: 0 引用数: 0 h-index: 0机构: Royal Adelaide Hosp, Dept Haematol, Adelaide, SA, Australia Univ Adelaide, Adelaide, SA, Australia Irish Haemophilia Soc, Dublin, IrelandGiermasz, Adam论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Hemophilia Treatment Ctr, Sacramento, CA USA Irish Haemophilia Soc, Dublin, IrelandTran, Huyen论文数: 0 引用数: 0 h-index: 0机构: Alfred Hosp, Haemophilia Treatment Ctr, Haemostasis & Thrombosis Unit, Melbourne, Vic, Australia Irish Haemophilia Soc, Dublin, IrelandKhoo, Teh -Liane论文数: 0 引用数: 0 h-index: 0机构: Royal Prince Alfred Hosp, Inst Haematol, Camperdown, NSW, Australia Irish Haemophilia Soc, Dublin, IrelandCockrell, Erin论文数: 0 引用数: 0 h-index: 0机构: St Josephs Childrens Hosp, Pediat Hematol Oncol, Tampa, FL USA Irish Haemophilia Soc, Dublin, IrelandPepperell, Dominic论文数: 0 引用数: 0 h-index: 0机构: Fiona Stanley Hosp, Dept Haematol, Murdoch, WA, Australia Irish Haemophilia Soc, Dublin, IrelandChambost, Herve论文数: 0 引用数: 0 h-index: 0机构: La Timone Children Hosp, AP HM, Dept Pediat Gastroenterol & Hepatol Multidiscipli, Marseille, France Aix Marseille Univ, INSERM, INRA, C2VN, Marseille, France Irish Haemophilia Soc, Dublin, IrelandLopez Fernandez, Maria Fernanda论文数: 0 引用数: 0 h-index: 0机构: Complejo Hosp Univ A Coruna, La Coruna, Spain Irish Haemophilia Soc, Dublin, IrelandKazmi, Rashid论文数: 0 引用数: 0 h-index: 0机构: Southampton Univ Hosp, Dept Haematol, Southampton, Hants, England Irish Haemophilia Soc, Dublin, IrelandMajerus, Elaine论文数: 0 引用数: 0 h-index: 0机构: Washington Univ St Louis, Dept Med, St Louis, MO USA Irish Haemophilia Soc, Dublin, Ireland论文数: 引用数: h-index:机构:Klamroth, Robert论文数: 0 引用数: 0 h-index: 0机构: Vivantes Klinikum Friedrichshain, Dept Obstet & Gynecol, Berlin, Germany Univ Bonn, Univ Hosp Bonn, Inst Expt Hematol & Transfus Med, Med Fac, Bonn, Germany Irish Haemophilia Soc, Dublin, IrelandQuinn, Jennifer论文数: 0 引用数: 0 h-index: 0机构: BioMarin UK Ltd, London, England Irish Haemophilia Soc, Dublin, IrelandYu, Hua论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Irish Haemophilia Soc, Dublin, IrelandWong, Wing Yen论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Irish Haemophilia Soc, Dublin, IrelandRobinson, Tara M.论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Irish Haemophilia Soc, Dublin, IrelandPipe, Steven W.论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Dept Pathol, Ann Arbor, MI USA Univ Michigan, Dept Pediat, Ann Arbor, MI USA Irish Haemophilia Soc, Dublin, Ireland
- [9] Transitioning patients with severe haemophilia A from emicizumab prophylaxis to valoctocogene roxaparvovec gene therapy: Real-world clinical experienceHAEMOPHILIA, 2024, 30 (05) : 1247 - 1249Klamroth, Robert论文数: 0 引用数: 0 h-index: 0机构: Vivantes Clin Friedrichshain, Internal Med Vasc Med & Haemostaseol, Berlin, Germany Univ Bonn, Univ Hosp Bonn, Inst Expt Hematol & Transfus Med, Med Fac, Bonn, Germany Univ Bonn, Med Fac, Bonn, Germany Vivantes Clin Friedrichshain, Internal Med Vasc Med & Haemostaseol, Berlin, GermanyGottstein, Saskia论文数: 0 引用数: 0 h-index: 0机构: Vivantes Clin Friedrichshain, Internal Med Vasc Med & Haemostaseol, Berlin, Germany Vivantes Clin Friedrichshain, Internal Med Vasc Med & Haemostaseol, Berlin, Germany
- [10] Efficacy, safety, and quality of life 4 years after valoctocogene roxaparvovec gene transfer for severe hemophilia A in the phase 3 GENEr8-1 trialRESEARCH AND PRACTICE IN THROMBOSIS AND HAEMOSTASIS, 2024, 8 (08)Leavitt, Andrew D.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USA Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USA论文数: 引用数: h-index:机构:Raheja, Priyanka论文数: 0 引用数: 0 h-index: 0机构: Royal London Hosp, Barts Hlth Natl Hlth Serv Trust, Haemophilia Ctr, London, England Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USASymington, Emily论文数: 0 引用数: 0 h-index: 0机构: Cambridge Univ Hosp, Natl Hlth Serv Fdn Trust, Cambridge, England Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USAV. Quon, Doris论文数: 0 引用数: 0 h-index: 0机构: Orthopaed Hemophilia Treatment Ctr, Los Angeles, CA USA Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USAGiermasz, Adam论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Davis, Hemophilia Treatment Ctr, Sacramento, CA USA Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USAFernandez, Maria Fernanda Lopez论文数: 0 引用数: 0 h-index: 0机构: Complejo Hosp Univ A Coruna, Almeria, Spain Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USAKenet, Gili论文数: 0 引用数: 0 h-index: 0机构: Tel Aviv Univ, Natl Hemophilia Ctr, Tel Aviv, Israel Tel Aviv Univ, Amalia Biron Res Inst Thrombosis & Hemostasis, Sheba Med Ctr, Tel Aviv, Israel Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USALowe, Gillian论文数: 0 引用数: 0 h-index: 0机构: Univ Hosp Birmingham, Natl Hlth Serv Fdn Trust, West Midlands Adult Haemophilia Comprehens Care Ct, Birmingham, England Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USAKey, Nigel S.论文数: 0 引用数: 0 h-index: 0机构: Univ N Carolina, Blood Res Ctr, Chapel Hill, NC USA Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USAMillar, Carolyn M.论文数: 0 引用数: 0 h-index: 0机构: Imperial Coll London, Ctr Haematol, London, England Imperial Coll Healthcare Natl Hlth Serv Trust, London, England Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USAPipe, Steven W.论文数: 0 引用数: 0 h-index: 0机构: Univ Michigan, Dept Pediat, Ann Arbor, MI USA Univ Michigan, Dept Pathol, Ann Arbor, MI USA Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USAMadan, Bella论文数: 0 引用数: 0 h-index: 0机构: Guys & St Thomas Natl Hlth Serv Fdn Trust, London, England Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USAChou, Sheng-Chieh论文数: 0 引用数: 0 h-index: 0机构: Natl Taiwan Univ Hosp, Dept Internal Med, Div Hematol, Taipei, Taiwan Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USAKlamroth, Robert论文数: 0 引用数: 0 h-index: 0机构: Vivantes Klinikum Friedrichshain, Padiatr Intens Med, Berlin, Germany Univ Bonn, Univ Hosp Bonn, Inst Expt Hematol & Transfus Med, Med Fac, Bonn, Germany Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USAMason, Jane论文数: 0 引用数: 0 h-index: 0机构: Royal Brisbane & Womens Hosp, Canc Care Serv, Queensland Haemophilia Ctr, Brisbane, Qld, Australia Univ Queensland, Brisbane, Qld, Australia Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USAChambost, Herve论文数: 0 引用数: 0 h-index: 0机构: Children Hosp La Timone, Assistance Publ Hop Marseille, Dept Pediat Immunol Hematol & Oncol, Marseille, France Aix Marseille Univ, Inst Natl Sante & Rech Med, Inst Natl Rech Agron, Ctr Rech Cardiovasc & Nutr, Marseille, France Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USA论文数: 引用数: h-index:机构:Majerus, Elaine论文数: 0 引用数: 0 h-index: 0机构: Washington Univ St Louis, Dept Med, St Louis, MO USA Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USAPepperell, Dominic论文数: 0 引用数: 0 h-index: 0机构: Fiona Stanley Hosp, Dept Haematol, Murdoch, WA, Australia Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USARivat, Christine论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USAYu, Hua论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USARobinson, Tara M.论文数: 0 引用数: 0 h-index: 0机构: BioMarin Pharmaceut Inc, Novato, CA USA Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USAOzelo, Margareth C.论文数: 0 引用数: 0 h-index: 0机构: Univ Estadual Campinas, Hemocentro Univ Campinas, Sch Med Sci, Dept Internal Med, Campinas, SP, Brazil Univ Calif San Francisco, Adult Hemophilia Treatment Ctr, Dept Med, 513 Parnassus Ave,Med Sci Bldg,Room S-561, San Francisco, CA 94143 USA