[1] Div Inherited Metab Dis, Heidelberg, Germany
[2] Univ Childrens Hosp Zurich, Div Metab, Zurich, Switzerland
[3] Washington State Univ, Coll Pharm, Pullman, WA 99164 USA
[4] Univ Amsterdam, Acad Med Ctr, Lab Genet Metab Dis, NL-1105 AZ Amsterdam, Netherlands
[5] Bambino Gesu Pediat Hosp, Neuropediat Dept, Rome, Italy