[1] Sapienza Univ Rome, Dept Pediat, Rome, Italy
[2] IRCCS Bambino Gesu Childrens Hosp, Dept Pediat Hematol Oncol, Rome, Italy
[3] Cincinnati Childrens Hosp Med Ctr, Dept Pediat, Div Immunobiol, Cincinnati, OH 45229 USA
[4] Cincinnati Childrens Hosp Med Ctr, Dept Pediat, Div Bone Marrow Transplantat & Immune Deficiency, Cincinnati, OH 45229 USA
[5] Univ Cincinnati, Coll Med, Cincinnati, OH USA
[6] Texas Childrens Hosp, Baylor Coll Med, Dept Pediat, Houston, TX 77030 USA
[7] Azienda Osped Univ Integrata, Woman & Child Hosp, Pediat Hematol Oncol, Verona, Italy
[8] Univ Milano Bicocca, Pediat Hematol Oncol Unit, Monza Brianza Bambino Mamma Fdn, Monza, Italy
[9] Great Ormond St Hosp Sick Children, Dept Hematol, London, England
[10] Dana Farber Boston Childrens Canc & Blood Disorde, Dept Pediat Hematol Oncol, Boston, MA USA
[11] Childrens Hosp Colorado, Ctr Canc & Blood Disorders, Aurora, CO USA
[12] Fdn Invest Biomed Hosp Infantil Univ Nino Jesus, Ctr Invest Biomed Red Enfermedades Raras, Dept Pediat Hematol Oncol, Madrid, Spain
[13] Fdn Invest Biomed Hosp Infantil Univ Nino Jesus, Ctr Invest Biomed Red Enfermedades Raras, Dept Hematol & Oncol, Madrid, Spain
[14] Univ Hosp Padova, Clin Pediat Hematol Oncol, Padua, Italy
[15] Regina Margherita Hosp, Div Pediat Oncohematol, Turin, Italy
[16] Univ Childrens Hosp, Dept Pediat Hematol & Oncol, Munster, Germany
[17] Hosp Univ Vall dHebron, Dept Pediat Hematol & Oncol, Barcelona, Spain
[18] Phoenix Childrens Hosp, Ctr Canc & Blood Disorders, Phoenix, AZ USA
[19] IRCCS Bambino Gesu Childrens Hosp, Div Rheumatol, Rome, Italy
[20] Cincinnati Childrens Hosp Med Ctr, Div Rheumatol, Cincinnati, OH 45229 USA
[21] MnS Modelling & Simulat, Dinant, Belgium
[22] Swedish Orphan BiovitrumAG Sobi, Basel, Switzerland
[23] Swedish Orphan Biovitrum AG Sobi, Basel, Switzerland