EFFICACY AND SAFETY OF EMAPALUMAB, A FULLY HUMAN, ANTI-INTERFERON GAMMA MONOCLONAL ANTIBODY, DESCRIBED IN TREATMENT-NAIVE PATIENTS WITH PRIMARY HEMOPHAGOCYTIC LYMPHOHISTOCYTOSIS

被引:0
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作者
Locatelli, Franco [1 ,2 ]
Jordan, Michael [3 ,4 ,5 ]
Allen, Carl [6 ]
Cesaro, Simone [7 ]
Rizzari, Carmelo [8 ]
Rao, Anupama [9 ]
Degar, Barbara [10 ]
Garrington, Timothy [11 ]
Sevilla, Julian [12 ,13 ]
Putti, Maria Caterina [14 ]
Fagioli, Franca [15 ]
Ahlmann, Martina [16 ]
Dapena Diaz, Jose-Luis [17 ]
Henry, Michael [18 ]
De Benedetti, Fabrizio [19 ]
Grom, Alexei [20 ]
Jacqmin, Philippe [21 ]
Ballabio, Maria [22 ]
de Min, Cristina [23 ]
机构
[1] Sapienza Univ Rome, Dept Pediat, Rome, Italy
[2] IRCCS Bambino Gesu Childrens Hosp, Dept Pediat Hematol Oncol, Rome, Italy
[3] Cincinnati Childrens Hosp Med Ctr, Dept Pediat, Div Immunobiol, Cincinnati, OH 45229 USA
[4] Cincinnati Childrens Hosp Med Ctr, Dept Pediat, Div Bone Marrow Transplantat & Immune Deficiency, Cincinnati, OH 45229 USA
[5] Univ Cincinnati, Coll Med, Cincinnati, OH USA
[6] Texas Childrens Hosp, Baylor Coll Med, Dept Pediat, Houston, TX 77030 USA
[7] Azienda Osped Univ Integrata, Woman & Child Hosp, Pediat Hematol Oncol, Verona, Italy
[8] Univ Milano Bicocca, Pediat Hematol Oncol Unit, Monza Brianza Bambino Mamma Fdn, Monza, Italy
[9] Great Ormond St Hosp Sick Children, Dept Hematol, London, England
[10] Dana Farber Boston Childrens Canc & Blood Disorde, Dept Pediat Hematol Oncol, Boston, MA USA
[11] Childrens Hosp Colorado, Ctr Canc & Blood Disorders, Aurora, CO USA
[12] Fdn Invest Biomed Hosp Infantil Univ Nino Jesus, Ctr Invest Biomed Red Enfermedades Raras, Dept Pediat Hematol Oncol, Madrid, Spain
[13] Fdn Invest Biomed Hosp Infantil Univ Nino Jesus, Ctr Invest Biomed Red Enfermedades Raras, Dept Hematol & Oncol, Madrid, Spain
[14] Univ Hosp Padova, Clin Pediat Hematol Oncol, Padua, Italy
[15] Regina Margherita Hosp, Div Pediat Oncohematol, Turin, Italy
[16] Univ Childrens Hosp, Dept Pediat Hematol & Oncol, Munster, Germany
[17] Hosp Univ Vall dHebron, Dept Pediat Hematol & Oncol, Barcelona, Spain
[18] Phoenix Childrens Hosp, Ctr Canc & Blood Disorders, Phoenix, AZ USA
[19] IRCCS Bambino Gesu Childrens Hosp, Div Rheumatol, Rome, Italy
[20] Cincinnati Childrens Hosp Med Ctr, Div Rheumatol, Cincinnati, OH 45229 USA
[21] MnS Modelling & Simulat, Dinant, Belgium
[22] Swedish Orphan BiovitrumAG Sobi, Basel, Switzerland
[23] Swedish Orphan Biovitrum AG Sobi, Basel, Switzerland
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中图分类号
R73 [肿瘤学];
学科分类号
100214 ;
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页数:2
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