AAV-Mediated Phenotypic Correction of the CNS Manifestations of a Mouse Model of Mucopolysaccharidosis Type I

被引：0
|
作者：
Van de Graaf, Benjamin G. [1 ]
Wang, Marlene [1 ]
Kwaa, Abena [1 ]
Hackett, Neil R. [1 ]
Crystal, Ronald G. [1 ]
Sondhi, Dolan [1 ]
机构：
[1] Weill Cornell Med Coll, New York, NY USA
来源：
MOLECULAR THERAPY | 2014年 / 22卷
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
384
引用
收藏
页码：S146 / S147
页数：2
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