SINGLE CELL ANALYSIS OF LENTIVIRAL INTEGRATION TO SUPPORT EX-VIVO GENE MODIFIED CELL THERAPY DEVELOPMENT

被引:0
|
作者
Di Cerbo, V. [1 ]
Santeramo, I. [1 ]
Hassan, E. [1 ]
Surmacz-Cordle, B. [1 ]
Marshall, D. [1 ]
机构
[1] Cell & Gene Therapy Catapult, London, England
关键词
D O I
10.1016/j.jcyt.2018.02.035
中图分类号
Q813 [细胞工程];
学科分类号
摘要
29
引用
收藏
页码:S18 / S18
页数:1
相关论文
共 50 条
  • [21] Ex-vivo analysis of programmed cell death on fibrolamellar carcinoma
    Ajay, Olutani-Grace
    Kent, Paul
    Nagourney, Robert Alan
    Stockwell, Tom
    Ellison, Jessica
    Swasey, Susanne M.
    Tasse, Jordan C.
    Schadde, Erik
    Humar, Abhinav
    Kato, Tom
    Yamashiro, Darrell
    JOURNAL OF CLINICAL ONCOLOGY, 2023, 41 (16)
  • [22] A single epidermal stem cell strategy for safe ex vivo gene therapy
    Lathion, Stephanie Droz-Georget
    Rochat, Ariane
    Knott, Graham
    Recchia, Alessandra
    Martinet, Danielle
    Benmohammed, Sara
    Grasset, Nicolas
    Zaffalon, Andrea
    Schmutz, Nathalie Besuchet
    Savioz-Dayer, Emmanuelle
    Beckmann, Jacques Samuel
    Rougemont, Jacques
    Mavilio, Fulvio
    Barrandon, Yann
    EMBO MOLECULAR MEDICINE, 2015, 7 (04) : 380 - 393
  • [23] INTERIM ANALYSIS ON NEUROLOGICAL OUTCOMES IN HURLER SYNDROME PATIENTS TREATED WITH EX-VIVO HAEMATOPOIETIC STEM CELL GENE THERAPY
    Consiglieri, Giulia
    Fumagalli, Francesca
    Tucci, Francesca
    Filisetti, Chiara
    Cossutta, Matilde
    Scarparo, Stefano
    Sarzana, Marina
    Puricelli, Cristina
    Ciotti, Francesca
    Barbera, Maurizio
    Darin, Silvia
    Parini, Rossella
    Baldoli, Cristina
    Gentner, Bernhard
    Aiuti, Alessandro
    Bernardo, Maria Ester
    BONE MARROW TRANSPLANTATION, 2024, 59 : 67 - 68
  • [24] AN EX-VIVO MODEL OF RADIAL GLIAL CELL DEVELOPMENT IN THE SPINAL CORD
    Pakan, J.
    McDermott, K.
    GLIA, 2013, 61 : S51 - S51
  • [25] The effects of in vivo B-cell depleting therapy on ex-vivo cytokine production
    Smeekens, Sanne P.
    van den Hoogen, Martijn W. F.
    Kamburova, Elena G.
    van de Veerdonk, Frank L.
    Joosten, Irma
    Koenen, Hans J. M. P.
    Netea, Mihai G.
    Hilbrands, Luuk B.
    Joosten, Leo A. B.
    TRANSPLANT IMMUNOLOGY, 2013, 28 (04) : 183 - 188
  • [26] Successful ex-vivo, gene therapy of recessive DEB
    Meneguzzi, G.
    Pin, D.
    Carozzo, C.
    Gache, Y.
    JOURNAL OF INVESTIGATIVE DERMATOLOGY, 2008, 128 : S124 - S124
  • [27] Clinical trial update: Ex-vivo autologous hematopoietic stem cell gene therapy in MPS IIIA
    Jones, Simon A.
    Kinsella, Jane L.
    Potter, Jane
    Thrasher, Adrian
    Booth, Claire
    Buckland, Karen
    Izotova, Natalia
    Rust, Stewart
    Weisberg, Daniel
    Church, Heather
    Tylee, Karen
    Lee, Helena
    Ford, Laura
    Holley, Rebecca J.
    Ellison, Stuart
    Bigger, Brian W.
    Wynn, Robert F.
    MOLECULAR GENETICS AND METABOLISM, 2022, 135 (02) : S63 - S64
  • [28] Lentiviral ex vivo gene therapy to the murine model of MPSII
    Wakabayashi, Taichi
    Kobayashi, Hiroshi
    Shimada, Yohta
    Higuchi, Takashi
    Eto, Yoshikatsu
    Ida, Hiroyuki
    Ohashi, Toya
    HUMAN GENE THERAPY, 2014, 25 (11) : A64 - A64
  • [29] Ex vivo lentiviral gene therapy for mucopolysaccharidosis type IVA
    Celik, Betul
    Rintz, Estera
    Nidhi, Fnu
    Khan, Shaukat
    Tomatsu, Shunji
    MOLECULAR GENETICS AND METABOLISM, 2024, 141 (02)
  • [30] Development of an Optimized Lentiviral Transduction Process for Ex Vivo CD34+Hematopoietic Stem Cell Gene Therapy Drug Product Manufacture
    Elavazhagan, Saranya
    Masdeu, Maria del Mar
    Zabinski, Tomasz
    Du, Lily
    Enjalbert, Florence
    Pennucci, Valentina
    Rana, Batika
    Whiting, Christopher
    Recchi, Chiara
    Heal, Paul
    Thrasher, Adrian J.
    Carbonaro-Sarracino, Denise A.
    Wolfe, Jia
    Gaspar, Bobby
    Sagoo, Pervinder
    MOLECULAR THERAPY, 2021, 29 (04) : 1 - 1