共 50 条
- [38] Spliceosome-Mediated Pre-mRNA trans-Splicing Can Repair CEP290 mRNA MOLECULAR THERAPY-NUCLEIC ACIDS, 2018, 12 : 294 - 308
- [40] Repair of Mybpc3 mRNA by 5′-trans-splicing in a Mouse Model of Hypertrophic Cardiomyopathy MOLECULAR THERAPY-NUCLEIC ACIDS, 2013, 2