[1] Our Ladys Childrens Hosp, Dublin, Ireland
[2] Univ Southern Calif, Keck Sch Med, Childrens Hosp Los Angeles, Los Angeles, CA USA
[3] Univ Witwatersrand, Fac Hlth Sci, Johannesburg, South Africa
[4] Univ Witwatersrand, Natl Hlth Lab Serv, Johannesburg, South Africa
[5] Great Ormond St Hosp Sick Children, London, England
[6] Barts & London Comprehens Care Ctr, London, England
[7] Biogen, Cambridge, MA USA
[8] Sobi, Stockholm, Sweden
[9] Univ Copenhagen, Copenhagen, Denmark