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- [11] Garetosmab in fibrodysplasia ossificans progressiva: a randomized, double-blind, placebo-controlled phase 2 trialNATURE MEDICINE, 2023, 29 (10) : 2615 - +Di Rocco, Maja论文数: 0 引用数: 0 h-index: 0机构: IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, Italy IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyForleo-Neto, Eduardo论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyPignolo, Robert J.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Dept Med, Rochester, MN USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyKeen, Richard论文数: 0 引用数: 0 h-index: 0机构: Royal Natl Orthopaed Hosp NHS Trust, Ctr Metab Bone Dis, London, England IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, Italy论文数: 引用数: h-index:机构:论文数: 引用数: h-index:机构:Roux, Christian论文数: 0 引用数: 0 h-index: 0机构: Cochin Hosp, Assistance Publ Hop Paris, Dept Rheumatol, Paris, France IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyKolta, Sami论文数: 0 引用数: 0 h-index: 0机构: Cochin Hosp, Assistance Publ Hop Paris, Dept Rheumatol, Paris, France IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyMadeo, Annalisa论文数: 0 引用数: 0 h-index: 0机构: IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, Italy IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyBubbear, Judith S.论文数: 0 引用数: 0 h-index: 0机构: Royal Natl Orthopaed Hosp NHS Trust, Ctr Metab Bone Dis, London, England IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyTabarkiewicz, Jacek论文数: 0 引用数: 0 h-index: 0机构: Rzeszow Univ, Med Coll, Inst Med Sci, Rzeszow, Poland IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalySzczepanek, Malgorzata论文数: 0 引用数: 0 h-index: 0机构: Rzeszow Univ, Med Coll, Inst Med Sci, Rzeszow, Poland IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyBachiller-Corral, Javier论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Ramon & Cajal, Dept Rheumatol, Madrid, Spain IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyCheung, Angela M.论文数: 0 引用数: 0 h-index: 0机构: Univ Toronto, Univ Hlth Network, Toronto, ON, Canada IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyDahir, Kathryn M.论文数: 0 引用数: 0 h-index: 0机构: Vanderbilt Univ, Med Ctr, Program Metab Bone Disorders, Nashville, TN USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyBotman, Esmee论文数: 0 引用数: 0 h-index: 0机构: Vrije Univ, Amsterdam Univ Med Ctr UMC, Amsterdam UMC Expert Ctr Rare Bone Dis, Dept Endocrinol & Metab, Amsterdam, Netherlands IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyRaijmakers, Pieter G.论文数: 0 引用数: 0 h-index: 0机构: Vrije Univ, Dept Radiol & Nucl Med, Amsterdam UMC, Amsterdam, Netherlands IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyMukaddam, Mona Al论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Orthopaed Med, Philadelphia, PA USA Univ Penn, Perelman Sch Med, Ctr Res FOP & Related Disorders, Philadelphia, PA USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyTile, Lianne论文数: 0 引用数: 0 h-index: 0机构: Univ Toronto, Univ Hlth Network, Toronto, ON, Canada IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyPortal-Celhay, Cynthia论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalySarkar, Neena论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyHou, Peijie论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyMusser, Bret J.论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyBoyapati, Anita论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyMohammadi, Kusha论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyMellis, Scott J.论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyRankin, Andrew J.论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyEconomides, Aris N.论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyTrotter, Dinko Gonzalez论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyHerman, Gary A.论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyO'Meara, Sarah J.论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyDelgizzi, Richard论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyWeinreich, David M.论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyYancopoulos, George D.论文数: 0 引用数: 0 h-index: 0机构: Regeneron Pharmaceut, Tarrytown, NY 10591 USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyEekhoff, E. Marelise W.论文数: 0 引用数: 0 h-index: 0机构: Vrije Univ, Amsterdam Univ Med Ctr UMC, Amsterdam UMC Expert Ctr Rare Bone Dis, Dept Endocrinol & Metab, Amsterdam, Netherlands IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, ItalyKaplan, Frederick S.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Perelman Sch Med, Dept Orthopaed Med, Philadelphia, PA USA Univ Penn, Perelman Sch Med, Ctr Res FOP & Related Disorders, Philadelphia, PA USA IRCCS Ist Giannina Gaslini, Dept Pediat, Unit Rare Dis, Genoa, Italy
- [12] Garetosmab in fibrodysplasia ossificans progressiva: a randomized, double-blind, placebo-controlled phase 2 trialNature Medicine, 2023, 29 : 2615 - 2624Maja Di Rocco论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsEduardo Forleo-Neto论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsRobert J. Pignolo论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsRichard Keen论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsPhilippe Orcel论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsThomas Funck-Brentano论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsChristian Roux论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsSami Kolta论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsAnnalisa Madeo论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsJudith S. Bubbear论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsJacek Tabarkiewicz论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsMałgorzata Szczepanek论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsJavier Bachiller-Corral论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsAngela M. Cheung论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsKathryn M. Dahir论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsEsmée Botman论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsPieter G. Raijmakers论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsMona Al Mukaddam论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsLianne Tile论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsCynthia Portal-Celhay论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsNeena Sarkar论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsPeijie Hou论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsBret J. Musser论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsAnita Boyapati论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsKusha Mohammadi论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsScott J. Mellis论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsAndrew J. Rankin论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsAris N. Economides论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsDinko Gonzalez Trotter论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsGary A. Herman论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsSarah J. O’Meara论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsRichard DelGizzi论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsDavid M. Weinreich论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsGeorge D. Yancopoulos论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsE. Marelise W. Eekhoff论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of PediatricsFrederick S. Kaplan论文数: 0 引用数: 0 h-index: 0机构: Unit of Rare Diseases,Department of Pediatrics
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