Review of CSF and Peripheral Immune Responses Following Intrathecal Gene Transfer for Giant Axonal Neuropathy

被引：0

作者：

Saade, Dimah ^{[1
]}

Bharucha-Goebel, Diana ^{[1
,2
]}

Foley, A. Reghan ^{[1
]}

Neuhaus, Sarah B. ^{[1
]}

Soldatos, Ariane ^{[3
]}

Hu, Ying ^{[1
]}

Hewitt, Matthew ^{[4
]}

Del Hoyo, Roberto Calcedo ^{[5
]}

Jacobson, Steven ^{[6
]}

Leibovitch, Emily ^{[6
]}

Nath, Avindra ^{[7
]}

Bailey, Rachel M. ^{[8
]}

Grieger, Josh ^{[9
]}

Samulski, R. Jude ^{[9
]}

Gray, Steven J. ^{[10
]}

Bonnemann, Carsten G. ^{[1
]}

机构：

[1] NINDS, Neuromusuclar & Neurogenet Disorders Childhood Se, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

[2] Childrens Natl Hlth Syst, Neurol, Washington, DC USA

[3] NINDS, Pediat Neurol, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

[4] Univ Penn, Gene Therapy Program, Immunol Core, Philadelphia, PA 19104 USA

[5] Univ Penn, Immunol Core, Philadelphia, PA 19104 USA

[6] NINDS, Neuroimmunol & Neurovirol, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

[7] NINDS, Sect Infect Nervous Syst, NIH, Bldg 36,Rm 4D04, Bethesda, MD 20892 USA

[8] Univ N Carolina, Gene Therapy Ctr, Chapel Hill, NC 27515 USA

[9] Bamboo Therapeut, Chapel Hill, NC USA

[10] Univ Texas Southwestern Med Ctr Dallas, Dept Pediat, Dallas, TX USA

来源：

MOLECULAR THERAPY | 2018年 / 26卷 / 05期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

999

引用

页码：456 / 457

页数：2

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