The application of bypassing-agent prophylaxis in haemophilia A patients with inhibitors: a meeting report

被引:10
|
作者
Valentino, L. A. [1 ,2 ]
Carcao, M. [3 ]
Mathew, P. [4 ]
Leissinger, C. A. [5 ]
Berntorp, E. [6 ]
Blanchette, V. [3 ]
Escuriola-Ettingshausen, C. [7 ]
Ewenstein, B. [8 ]
Ewing, N. [9 ]
Gringeri, A. [10 ]
Hoots, W. K. [11 ]
Negrier, C. [12 ]
机构
[1] Rush Univ, Med Ctr, Hemophilia & Thrombophilia Ctr, Dept Pediat, Chicago, IL 60612 USA
[2] Rush Univ, Med Ctr, Dept Internal Med, Chicago, IL 60612 USA
[3] Hosp Sick Children, Dept Pediat, Toronto, ON M5G 1X8, Canada
[4] Univ New Mexico, Dept Pediat, Hlth Sci Ctr, Albuquerque, NM 87131 USA
[5] Tulane Univ, Med Ctr, Louisiana Ctr Bleeding & Clotting, New Orleans, LA USA
[6] Malmo Univ Hosp, Dept Coagulat Disorders, Malmo, Sweden
[7] JW Goethe Univ Hosp, Dept Pediat, Franklin, Germany
[8] Baxter Biosci, Westlake Village, CA USA
[9] City Hope Natl Med Ctr, Div Pediat, Duarte, CA 91010 USA
[10] Univ Milan, A Bianchi Bonomi Hemophilia & Thrombosis Ctr, I-20122 Milan, Italy
[11] Univ Texas Med Sch, Dept Pediat, Houston, TX USA
[12] Hop Edouard Herriot, Hemophilia Ctr, Lyon, France
关键词
PROTHROMBIN COMPLEX CONCENTRATE; HIGH-RESPONDING INHIBITORS; RECOMBINANT FACTOR-VIIA; IMMUNE TOLERANCE; ACTIVITY FEIBA; INTRACRANIAL HEMORRHAGE; BLEEDING EPISODES; THERAPY; SAFETY; POPULATION;
D O I
10.1111/j.1365-2516.2008.01953.x
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:959 / 965
页数:7
相关论文
共 50 条
  • [31] THE SEQUENTIAL COMBINED BYPASSING THERAPY IS EFFECTIVE AND SAFE IN THE TREATMENT OF UNRESPONSIVE BLEEDS IN HAEMOPHILIA PATIENTS WITH INHIBITORS
    Gringeri, A.
    Fischer, K.
    Karafoulidou, A.
    Lopez-Fernandez, M. F.
    HAEMATOLOGICA-THE HEMATOLOGY JOURNAL, 2009, 94 : 42 - 42
  • [32] Effect of bypassing agent therapy with and without tranexamic acid in haemophilia A patients with inhibitors, a prospective crossover study using thromboelastography and thrombin generation assay
    Tran, H. T. T.
    Sorensen, B.
    Rea, C.
    Bjornsen, S.
    Ueland, T.
    Pripp, A. H.
    Tjonnfjord, G.
    Holme, P. A.
    JOURNAL OF THROMBOSIS AND HAEMOSTASIS, 2013, 11 : 233 - 234
  • [33] Reply to 'Differential response to bypassing agents complicates treatment in patients with haemophilia and inhibitors' (Haemophilia 2009; 15: 3-10)
    Hedner, U.
    HAEMOPHILIA, 2010, 16 (02) : 372 - 373
  • [34] REAL-WORLD EFFICACY OF EMICIZUMAB PROPHYLAXIS IN PATIENTS WITH SEVERE HAEMOPHILIA A WITHOUT INHIBITORS: A REPORT FROM THE UK HAEMOPHILIA CENTRE DOCTORS' ORGANISATION
    Wall, C.
    Xiang, H.
    Palmer, B.
    Collins, P. W.
    Stephensen, D.
    Scott, M.
    Chalmers, E.
    Chowdary, P.
    Hall, G. W.
    Liesner, R.
    Hart, D. P.
    Shapiro, S.
    Talks, K.
    Fletcher, S.
    Hay, C. R.
    HAEMOPHILIA, 2021, 27 : 116 - 116
  • [35] Perioperative safety and haematostatic efficacy of a new bypassing agent pd-FVIIa/FX (Byclot) in haemophilia patients with high-responding type inhibitors
    Shirayama, Rie
    Takedani, Hideyuki
    Chikasawa, Yushi
    Ishiguro, Akira
    Ishimura, Masataka
    Isobe, Kiyotaka
    Uchiba, Mitsuhiro
    Ogata, Yoshiyasu
    Kakuda, Harumi
    Kusuhara, Koichi
    Shirahata, Akira
    BLOOD COAGULATION & FIBRINOLYSIS, 2019, 30 (08) : 385 - 392
  • [36] Cost-Effectiveness and Budget Impact of Emicizumab Prophylaxis in Haemophilia A Patients with Inhibitors
    Cortesi, Paolo Angelo
    Castaman, Giancarlo
    Trifiro, Gianluca
    Creazzola, Simona Serao
    Improta, Giovanni
    Mazzaglia, Giampiero
    Molinari, Angelo Claudio
    Mantovani, Lorenzo Giovanni
    THROMBOSIS AND HAEMOSTASIS, 2020, 120 (02) : 216 - 228
  • [37] Long term follow up of secondary prophylaxis with RFVIIA in haemophilia patients with inhibitors
    Torres, O. W.
    Nascimento, P. D.
    Arbesu, G.
    Borchichi, S.
    Buceta, A.
    JOURNAL OF THROMBOSIS AND HAEMOSTASIS, 2011, 9 : 368 - 369
  • [38] Immune tolerance induction in paediatric patients with haemophilia A and inhibitors receiving emicizumab prophylaxis
    Batsuli, Glaivy
    Zimowski, Karen L.
    Tickle, Kelly
    Meeks, Shannon L.
    Sidonio, Robert F., Jr.
    HAEMOPHILIA, 2019, 25 (05) : 789 - 796
  • [39] Successful major and minor surgery using factor VIII inhibitor bypassing activity in patients with haemophilia A and inhibitors
    Lauroua, P.
    Ferrer, A. -M.
    Guerin, V.
    HAEMOPHILIA, 2009, 15 (06) : 1300 - 1307
  • [40] Plasma-derived factor VIIa and factor X mixture agent (MC710) prophylaxis in haemophilia B patients with inhibitors
    Sakai, Michio
    Amano, Kagehiro
    Chin, Motoaki
    Takedani, Hideyuki
    Ishida, Hiroyuki
    Sakashita, Kazuo
    Taki, Masashi
    Migita, Masahiro
    Watanabe, Hiroyoshi
    Ishimura, Masataka
    Nogami, Keiji
    Harano, Sho
    Shirahata, Akira
    HAEMOPHILIA, 2023, 29 (02) : 456 - 465