Dose-response effect of RPE65 gene therapy on retinoid levels and correlation with clinical rescue in Rpe65-deficient dogs

被引：0
|
作者：
Mowat, Freya [1 ,2 ]
Feathers, Kecia L. [3 ]
Smith, Alexander J. [2 ,4 ]
Thompson, Debra A. [3 ]
Petersen-Jones, Simon M. [1 ]
Bainbridge, James W. B. [2 ,4 ]
Ali, Robin R. [2 ,4 ]
机构：
[1] Michigan State Univ, Coll Vet Med, Small Anim Clin Sci, E Lansing, MI 48824 USA
[2] UCL Inst Ophthalmol, London, England
[3] Univ Michigan, Dept Biol Chem, Dept Ophthalmol & Visual Sci, Ann Arbor, MI 48109 USA
[4] Biomed Res Ctr Ophthalmol Moorfields, Natl Inst Hlth Res, London, England
来源：
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE | 2015年 / 56卷 / 07期
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D O I：
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中图分类号：
R77 [眼科学];
学科分类号：
100212 ;
摘要：
2064
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页数：2
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