Non-viral DNA delivery associated to TALEN® gene editing leads to highly efficient correction of sickle cell mutation in long-term repopulating hematopoietic stem cells

被引：0
|
作者：
Moiani, A. [1 ]
Letort, G. [1 ]
Lizot, S. [1 ]
Hong, P. [1 ]
Temburni-Blake, S. [1 ]
Felix, T. [2 ]
Chalumeau, A. [2 ]
Miccio, A. [2 ]
Gouble, A. [1 ]
Juillerat, A. [1 ]
Duclert, A. [1 ]
Duchateau, P. [1 ]
Valton, J. [1 ]
机构：
[1] Cellectis Therapeut, Paris, France
[2] Imagine Inst, Paris, France
来源：
HUMAN GENE THERAPY | 2022年 / 33卷 / 23-24期
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D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
OR46
引用
收藏
页码：A17 / A17
页数：1
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