EFFICIENT GENE EDITING IN CD34+HEMATOPOIETIC STEM AND PROGENITOR CELLS USING NON-VIRAL LIPID NANOPARTICLES

被引:0
|
作者
Park, S. [1 ]
Balgi, A. [1 ]
Zhao, R. [1 ]
Swaminathan, M. [1 ]
Jain, N. [1 ]
Thomas, A. [1 ]
Zhang, A. [1 ]
Clarke, S. [1 ]
Geczy, R. [1 ]
机构
[1] Cytiva, R&D, Vancouver, BC, Canada
关键词
LNP; HSPC; Gene-Editing;
D O I
暂无
中图分类号
Q813 [细胞工程];
学科分类号
摘要
16
引用
收藏
页码:S16 / S16
页数:1
相关论文
共 50 条
  • [1] Efficient Gene Editing in CD34+Hematopoietic Stem and Progenitor Cells Using Non-Viral Lipid Nanoparticles
    Balgi, Aruna
    Park, Stella
    Zhao, Rita
    Swaminathan, Meenakshi
    Jain, Nikita
    Thomas, Anitha
    Clarke, Samuel
    Zhang, Angela
    Geczy, Reka
    MOLECULAR THERAPY, 2024, 32 (04) : 593 - 593
  • [2] LIPID NANOPARTICLES FOR CD34+HEMATOPOIETIC STEM AND PROGENITOR CELL GENE EDITING: EFFICIENT NON-VIRAL SOLUTIONS FOR ADVANCED CELLULAR THERAPIES
    Park, S.
    Balgi, A.
    Swaminathan, M.
    Zhao, R.
    Jain, N.
    Thomas, A.
    Zhang, A.
    Clarke, S.
    Geczy, R.
    CYTOTHERAPY, 2023, 25 (06) : S133 - S134
  • [3] Non-Viral RNA-Lipid Nanoparticles for High Efficiency Genome Editing of CD34+Hematopoietic Stem and Progenitor Cells for Advanced Cell and Gene Therapies
    Geczy, Reka
    Park, Stella
    Zhao, Rita
    Swaminathan, Meenakshi
    Jain, Nikita
    Thomas, Anitha
    Zhang, Angela
    Clarke, Samuel
    BLOOD, 2023, 142
  • [4] Non-Viral RNA-Lipid Nanoparticles for High Efficiency Genome Editing of CD34+Hematopoietic Stem and Progenitor Cells for Advanced Cell and Gene Therapies
    Clarke, Samuel
    Park, Stella
    Balgi, Aruna
    Zhao, Rita
    Swaminathan, Meenakshi
    Jain, Nikita
    Thomas, Anitha
    Zhang, Angela
    Geczy, Reka
    MOLECULAR THERAPY, 2023, 31 (04) : 714 - 714
  • [5] Highly Efficient Non-Viral Gene Editing of Unactivated Human T cells and Hematopoietic Stem and Progenitor Cells Using Microfluidic Transfection
    Ouellet, Eric
    Chehal, Manreet
    Lambertz, Ulrike
    Binson, Elinor
    Liao, Tina
    Paik, Gil
    Chau, Phillip
    Chen, Kevin
    Dalton, Bob
    Eaves, Allen C.
    Louis, Sharon A.
    Kokaji, Andy
    MOLECULAR THERAPY, 2024, 32 (04) : 814 - 814
  • [6] Improving lentiviral transduction of CD34+hematopoietic stem and progenitor cells
    Hauber, I.
    Beschorner, N.
    Schroedel, S.
    Chemnitz, J.
    Kroeger, N.
    Hauber, J.
    Ferreira, I. R. S.
    Thirion, C.
    HUMAN GENE THERAPY, 2019, 30 (08) : A23 - A23
  • [7] Non-peptide lipid mediators induce proliferation and adhesion of CD34+hematopoietic progenitor cells
    Boehmler, A
    Denzlinger, C
    Kanz, L
    Möhle, R
    EXPERIMENTAL HEMATOLOGY, 2002, 30 (06) : 128 - 128
  • [8] Molecular phenotype of malignant CD34+hematopoietic stem and progenitor cells in chronic myelogenous leukemia
    Kronenwett, R
    Diaz-Blanco, E
    Graef, T
    Steidl, U
    Kliszewski, S
    Bruns, I
    Neumann, F
    Bork, S
    Butterweck, U
    Roes, N
    Brors, B
    Eils, R
    Kobbe, G
    Gattermann, N
    Haas, R
    BLOOD, 2005, 106 (11) : 802A - 803A
  • [9] Neurobiological molecular phenotype of primary human CD34+hematopoietic stem and progenitor cells.
    Steidl, U
    Bork, S
    Schaub, S
    Selbach, O
    Seres, J
    Rohr, UP
    Fenk, R
    Schroeder, T
    Aivado, M
    Maercker, C
    Gattermann, N
    Bornstein, SR
    Haas, HL
    Haas, R
    Kronenwett, R
    BLOOD, 2003, 102 (11) : 332A - 332A
  • [10] Enhanced Lentiviral Vector Transduction of CD34+Hematopoietic Stem and Progenitor Cells by Targeting Anti-Viral Restriction Factors
    Leon-Rico, Diego
    Thorne, Lucy G.
    Diasakou, Argyro
    Graham, Ben
    Warne, Justin
    Alemayehu, Helen
    Selwood, David
    Towers, Greg J.
    Booth, Claire
    Thrasher, Adrian J.
    MOLECULAR THERAPY, 2020, 28 (04) : 66 - 66