FOXP3 Gene Transfer in T cells and FOXP3 Gene Editing in HSC as Novel Treatment Options for IPEX Syndrome

被引：0

作者：

Goodwin, Marianne ^{[1
]}

Sato, Yohei ^{[1
]}

Passerini, Laura ^{[2
]}

Barzaghi, Federica ^{[2
]}

Lee, Esmond ^{[3
]}

Suzette, Shipp K. ^{[1
]}

Roncarolo, Maria Grazia ^{[4
,5
,6
]}

Porteus, Matthew ^{[1
]}

Bacchetta, Rosa ^{[1
]}

机构：

[1] Stanford Univ, Sch Med, Dept Pediat, Div Stem Cell Transplantat & Regenerat Med, Stanford, CA 94305 USA

[2] Ist Sci San Raffaele, San Raffaele Telethon Inst Gene Therapy, Div Regenerat Med Stem Cells & Gene Therapy, Milan, Italy

[3] Stanford Univ, Sch Med, Inst Stem Cell Biol & Regenerat Med, Stanford, CA 94305 USA

[4] Stanford Univ, Sch Med, Pediat Stem Cell Transplantat & Regenerat Med & M, Stanford, CA 94305 USA

[5] Stanford Univ, Sch Med, Pediat Stem Cell Transplantat & Regenerat Med, Stanford, CA 94305 USA

[6] Stanford Univ, Sch Med, Div Stem Cell Transplantat & Regenerat Med, Ctr Definit & Curat Med,Dept Pediat, Stanford, CA 94305 USA

来源：

JOURNAL OF CLINICAL IMMUNOLOGY | 2018年 / 38卷 / 03期

关键词：

D O I：

暂无

中图分类号：

R392 [医学免疫学]; Q939.91 [免疫学];

学科分类号：

100102 ;

摘要：

引用

页码：427 / 427

页数：1

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