An adenoviral mediated gene therapy for mucopolysaccharidosis type I

被引：0
|
作者：
Hurt, Sarah [1 ]
Le, Steven Q. [1 ]
Mendonca, Samir [1 ]
Dickson, Patricia [1 ]
Curiel, David T. [1 ]
机构：
[1] Washington Univ St Louis, St Louis, MO USA
来源：
MOLECULAR GENETICS AND METABOLISM | 2022年 / 135卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2021.11.148
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
133
引用
收藏
页码：S60 / S60
页数：1
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