Gene therapy for Dopamine transporter deficiency syndrome: Infantile Parkinsonism-dystonia

被引：0

作者：

Ng, J. ^{[1
]}

Barral, S. ^{[1
]}

Barrigon, C. de la Fuente ^{[1
]}

Lignani, G. ^{[1
]}

Erdem, F. ^{[1
,2
]}

Wallings, R. ^{[3
]}

Privolizzi, R. ^{[1
]}

Rossignoli, G. ^{[1
]}

Al Rashidi, H. ^{[1
]}

Heasman, S. ^{[1
]}

Meyer, E. ^{[1
]}

Ngoh, A. ^{[1
]}

Pope, S.

Karda, R. ^{[1
]}

Perocheau, D. ^{[1
]}

Baruteau, J. ^{[1
,6
]}

Suff, N. ^{[1
,4
]}

Diaz, J. A. Antinao ^{[1
]}

Vowles, J. ^{[3
]}

Cowley, S. A. ^{[1
]}

Friessmuth, M. ^{[2
]}

Sucic, S. ^{[2
]}

Counsell, J. ^{[1
]}

Wade-Martins, R. ^{[3
]}

Heales, S. J. R. ^{[5
,6
]}

Rahim, A. A. ^{[1
]}

Bencze, M. ^{[1
]}

Waddington, S. N. ^{[1
]}

Kurian, M. A. ^{[1
,6
]}

机构：

[1] UCL, London, England

[2] Med Univ Vienna, Vienna, Austria

[3] Univ Oxford, Oxford, England

[4] Kings Coll London, London, England

[5] Natl Hosp Neurol & Neurosurg, London, England

[6] Great Ormond St Hosp Sick Children, London, England

来源：

HUMAN GENE THERAPY | 2021年 / 32卷 / 19-20期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

P070

引用

页码：A50 / A50

页数：1

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