机构:
US FDA, Off New Drugs, Rare Dis Program, Ctr Drug Evaluat & Res, Silver Spring, MD 20993 USAUS FDA, Off New Drugs, Rare Dis Program, Ctr Drug Evaluat & Res, Silver Spring, MD 20993 USA
Pariser, Anne R.
Gahl, William A.
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机构:
NIH, Undiagnosed Dis Program, Off Director, Bethesda, MD 20892 USA
NHGRI, NIH, Bethesda, MD 20892 USAUS FDA, Off New Drugs, Rare Dis Program, Ctr Drug Evaluat & Res, Silver Spring, MD 20993 USA