Repair of rhodopsin mRNA by spliceosome-mediated RNA trans-splicing in cell-lines expressing normal or mutant rhodopsin

被引：0
|
作者：
Berger, A. [1 ]
Lorain, S. [2 ]
Josephine, C. [3 ,4 ]
Desrosiers, M. [1 ]
Peccate, C. [2 ]
Voit, T. [2 ]
Garcia, L. [5 ]
Sahel, J. A. [1 ,6 ]
Bemelmans, A. P. [3 ,4 ]
机构：
[1] Univ Paris 06, Inst Vis, Paris, France
[2] Univ Paris 06, Inst Myol, Paris, France
[3] CEA, MIRCen, Paris, France
[4] CNRS, URA2210, Paris, France
[5] Univ Versailles St Quentin, Paris, France
[6] CHNO XV XX, Paris, France
来源：
HUMAN GENE THERAPY | 2014年 / 25卷 / 11期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P147
引用
收藏
页码：A103 / A103
页数：1
相关论文
共 50 条
  • [41] Correction of DNA protein kinase deficiency by spliceosome-mediated RNA trans-splicing and Sleeping Beauty transposon delivery
    Zayed, Hatem
    Xia, Lily
    Yerich, Anton
    Yant, Stephen R.
    Kay, Mark A.
    Puttaraju, M.
    McGarrity, Gerard J.
    Wiest, David L.
    McIvor, R. Scott
    Tolar, Jakub
    Blazar, Bruce R.
    MOLECULAR THERAPY, 2007, 15 (07) : 1273 - 1279
  • [42] 5′ exon replacement by spliceosome mediated RNA trans-splicing
    Mansfield, SG
    Hawkins-Clark, R
    Cohn, JA
    Kole, J
    Mitchell, LG
    Garcia-Blanco, MA
    MOLECULAR THERAPY, 2003, 7 (05) : S301 - S302
  • [43] Correction of tau mis-splicing caused by FTDP-17 MAPT mutations by spliceosome-mediated RNA trans-splicing
    Rodriguez-Martin, Teresa
    Anthony, Karen
    Garcia-Blanco, Mariano A.
    Mansfield, S. Gary
    Anderton, Brian H.
    Gallo, Jean-Marc
    HUMAN MOLECULAR GENETICS, 2009, 18 (17) : 3266 - 3273
  • [44] Promiscuity of pre-mRNA spliceosome-mediated trans splicing:: A problem for gene therapy?
    Kikumori, T
    Cote, GJ
    Gagel, RF
    HUMAN GENE THERAPY, 2001, 12 (11) : 1429 - 1441
  • [45] Imaging trans-splicing events in cells and living animals using the SMaRT™ (spliceosome mediated RNA trans-splicing) strategy
    Bhaumik, S
    Puttaraju, M
    Mitchell, LG
    Gambhir, SS
    MOLECULAR THERAPY, 2003, 7 (05) : S138 - S139
  • [46] Spliceosome Mediated RNA Trans-Splicing for Targeting Kappa+ B-Cell Neoplasms
    Weiss, Lukas
    Gruber, Christina
    Koller, Ulrich
    Pinon-Hofbauer, Josefina
    Hainzl, Stefan
    Hufnagl, Clemens
    Melchardt, Thomas
    Brachtl, Gabriele
    Greil, Richard
    Bauer, Johann
    Egle, Alexander
    BLOOD, 2014, 124 (21)
  • [47] Dysferlin rescue by spliceosome-mediated pre-mRNA trans-splicing targeting introns harbouring weakly defined 3' splice sites
    Philippi, Susanne
    Lorain, Stephanie
    Beley, Cyriaque
    Peccate, Cecile
    Precigout, Guillaume
    Spuler, Simone
    Garcia, Luis
    HUMAN MOLECULAR GENETICS, 2015, 24 (14) : 4049 - 4060
  • [48] Therapy of dominant Epidermolysis bullosa vie Spliceosome Mediated RNA Trans-splicing
    Wally, V
    Brunner, M.
    Koller, U.
    Hintner, H.
    Bauer, J. W.
    JOURNAL OF INVESTIGATIVE DERMATOLOGY, 2009, 129 : S55 - S55
  • [49] Partial correction of endogenous ΔF508 CFTR in human cystic fibrosis airway epithelia by spliceosome-mediated RNA trans-splicing
    Xiaoming Liu
    Qinshi Jiang
    S. Gary Mansfield
    M. Puttaraju
    Yulong Zhang
    Weihong Zhou
    Jonathan A. Cohn
    Mariano A. Garcia-Blanco
    Lloyd G. Mitchell
    John F. Engelhardt
    Nature Biotechnology, 2002, 20 : 47 - 52
  • [50] Partial correction of endogenous ΔF508 CFTR in human cystic fibrosis airway epithelia by spliceosome-mediated RNA trans-splicing
    Liu, XM
    Jiang, QS
    Mansfield, SG
    Puttaraju, M
    Zhang, YL
    Zhou, WH
    Cohn, JA
    Garcia-Blanco, MA
    Mitchell, LG
    Engelhardt, JF
    NATURE BIOTECHNOLOGY, 2002, 20 (01) : 47 - 52
12345