Investor Outlook: Solving Gene Therapy Pricing ... with a Cures Voucher?

被引:4
|
作者
Schimmer, Joshua [1 ]
Breazzano, Steven [1 ]
机构
[1] Piper Jaffray & Co, New York, NY USA
关键词
D O I
10.1089/humc.2016.29018.ind
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
Gene therapy reimbursement continues to be an intense topic of discussion in the field given the unique and durable benefits from a single administration and generally small patient populations against a reimbursement framework that is not optimized for such "cures" or long-lived benefits. As more gene therapy programs enter the market and late-stage development, it is increasingly important for the field to define a reimbursement model that works for all stakeholders in order to encourage the next wave of innovation. To add to the discussion around new payment models and potential solutions, we propose a flexible voucher system that takes advantage of existing infrastructure, precedent, and regulatory frameworks.
引用
收藏
页码:132 / 136
页数:5
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