Drug and Gene Delivery to the Back of the Eye: From Bench to Bedside

被引:90
|
作者
Rowe-Rendleman, Cheryl L. [1 ]
Durazo, Shelley A. [2 ]
Kompella, Uday B. [2 ]
Rittenhouse, Kay D. [3 ]
Di Polo, Adriana [4 ]
Weiner, Alan L. [5 ]
Grossniklaus, Hans E. [6 ]
Naash, Muna I. [7 ]
Lewin, Alfred S. [8 ]
Horsager, Alan [9 ]
Edelhauser, Henry F. [6 ]
机构
[1] Omar Consulting Grp LLC, Princeton Jct, NJ USA
[2] Univ Colorado, Aurora, CO 80045 USA
[3] Pfizer Inc, San Diego, CA USA
[4] Univ Montreal, Montreal, PQ, Canada
[5] DrugDel Consulting LLC, Arlington, TX USA
[6] Emory Univ, Ctr Eye, Atlanta, GA 30322 USA
[7] Univ Oklahoma, Hlth Sci Ctr, Oklahoma City, OK USA
[8] Univ Florida, Gainesville, FL USA
[9] Univ So Calif, Inst Med Genet, Los Angeles, CA USA
关键词
drug delivery; gene therapy; retina; nanoparticle; translational medicine; COMPACTED DNA-NANOPARTICLES; LEBER CONGENITAL AMAUROSIS; RETINAL GANGLION-CELLS; ADENOASSOCIATED VIRUS; DIPEPTIDE PRODRUGS; RPE65; MUTATIONS; VISUAL FUNCTION; THERAPY; MOUSE; PHARMACOKINETICS;
D O I
10.1167/iovs.13-13707
中图分类号
R77 [眼科学];
学科分类号
100212 ;
摘要
[No abstract available]
引用
收藏
页码:2714 / 2730
页数:17
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