Introduction of the TYMP Gene in Thymidine Phosphorylase Deficient Cell Lines Using Lentiviral Vectors Restores Enzyme Activity: Prospects for Gene Therapy of MNGIE (Mitochondrial Neurogastrointestinal Encephalomyopathy)

被引：0
|
作者：
Gomez, A.
Torres, J. [1 ]
Eixarch, H.
Andreu, A. L. [1 ]
Marti, R. [1 ]
Barquinero, J.
机构：
[1] Inst Salud Carlos III, Ctr Biomed Res Rare Dis CIBERER, Madrid, Spain
来源：
HUMAN GENE THERAPY | 2009年 / 20卷 / 09期
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D O I：
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中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
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页码：1083 / 1083
页数：1
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