Thymidine phosphorylase is both a therapeutic and a suicidal gene in a murine model of Mitochondrial Neurogastrointestinal Encephalomyopathy (MNGIE)

被引：0
|
作者：
Lopez-Estevez, S. [1 ]
Ferrer, G. [1 ]
Torres-Torronteras, J. [2 ,3 ]
Mansilla, M. J. [1 ]
Casacuberta-Serra, S. [1 ]
Martorell, L. [1 ]
Hirano, M. [4 ]
Marti, R. [2 ,3 ]
Barquinero, J. [1 ]
机构：
[1] Univ Autonoma Barcelona, Gene & Cell Therapy Lab, Vall dHebron Res Inst VHIR, E-08193 Barcelona, Spain
[2] VHIR, Mitochondrial Disorders Unit, Barcelona, Spain
[3] Ctr Biomed Network Res Rare Dis CIBERER, Barcelona, Spain
[4] Columbia Univ, Med Ctr, Dept Neurol, New York, NY 10032 USA
来源：
HUMAN GENE THERAPY | 2013年 / 24卷 / 12期
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中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
引用
收藏
页码：A137 / A137
页数：1
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