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- [41] Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich SyndromeSCIENCE, 2013, 341 (6148) : 865 - U71Aiuti, Alessandro论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, HSR TIGET Pediat Clin Res Unit, I-20132 Milan, Italy Ist Sci San Raffaele, Pediat Immunohematol & Bone Marrow Transplant Uni, I-20132 Milan, Italy Bambino Gesu Pediat Hosp, Univ Dept Pediat DPUO, I-00165 Rome, Italy Tor Vergata Univ, Sch Med, I-20132 Rome, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyBiasco, Luca论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyScaramuzza, Samantha论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyFerrua, Francesca论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, HSR TIGET Pediat Clin Res Unit, I-20132 Milan, Italy Ist Sci San Raffaele, Pediat Immunohematol & Bone Marrow Transplant Uni, I-20132 Milan, Italy Univ Vita Salute San Raffaele, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyCicalese, Maria Pia论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, HSR TIGET Pediat Clin Res Unit, I-20132 Milan, Italy Ist Sci San Raffaele, Pediat Immunohematol & Bone Marrow Transplant Uni, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyBaricordi, Cristina论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyDionisio, Francesca论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyCalabria, Andrea论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyGiannelli, Stefania论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyCastiello, Maria Carmina论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, Italy Univ Vita Salute San Raffaele, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyBosticardo, Marita论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyEvangelio, Costanza论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, HSR TIGET Pediat Clin Res Unit, I-20132 Milan, Italy Ist Sci San Raffaele, Pediat Immunohematol & Bone Marrow Transplant Uni, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyAssanelli, Andrea论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Pediat Immunohematol & Bone Marrow Transplant Uni, I-20132 Milan, Italy Ist Sci San Raffaele, Hematol & Bone Marrow Transplant Unit, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyCasiraghi, Miriam论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, HSR TIGET Pediat Clin Res Unit, I-20132 Milan, Italy Ist Sci San Raffaele, 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Gene Therapy HSR TIGET, I-20132 Milan, ItalyPellin, Danilo论文数: 0 引用数: 0 h-index: 0机构: Univ Vita Salute San Raffaele, Univ Ctr Stat Biomed Sci CUSSB, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyDi Serio, Clelia论文数: 0 引用数: 0 h-index: 0机构: Univ Vita Salute San Raffaele, Univ Ctr Stat Biomed Sci CUSSB, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalySchmidt, Manfred论文数: 0 引用数: 0 h-index: 0机构: Deutsch Krebsforschungszentrum, Nat Zentrum Tumorerkrankungen, D-69120 Heidelberg, Germany Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyVon Kalle, Christof论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy 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ItalyGaly, Anne论文数: 0 引用数: 0 h-index: 0机构: UMR 951, F-91002 Evry, France Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyMiniero, Roberto论文数: 0 引用数: 0 h-index: 0机构: Magna Graecia Univ Catanzaro, Dipartimento Sci Med Chirurg, I-88100 Catanzaro, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyFinocchi, Andrea论文数: 0 引用数: 0 h-index: 0机构: Tor Vergata Univ, Sch Med, I-20132 Rome, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyMetin, Ayse论文数: 0 引用数: 0 h-index: 0机构: Ankara Childrens Hosp, TR-06050 Ankara, Turkey Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyBanerjee, Pinaki P.论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyOrange, Jordan S.论文数: 0 引用数: 0 h-index: 0机构: Texas Childrens Hosp, Baylor Coll Med, Houston, TX 77030 USA Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, Italy论文数: 引用数: h-index:机构:Valsecchi, Maria Grazia论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Pediat Immunohematol & Bone Marrow Transplant Uni, I-20132 Milan, Italy Univ Milano Bicocca, Dipartimento Med Clin & Prevenzione, I-20126 Monza, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyBiffi, Alessandra论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, HSR TIGET Pediat Clin Res Unit, I-20132 Milan, Italy Ist Sci San Raffaele, Pediat Immunohematol & Bone Marrow Transplant Uni, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyMontini, Eugenio论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyVilla, Anna论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, Italy CNR, IRGB, I-20138 Milan, Italy Ist Sci San Raffaele, Div Regenerat Med Stem Cells & Gene Therapy, San Raffaele Telethon Inst Gene Therapy HSR TIGET, I-20132 Milan, ItalyCiceri, Fabio论文数: 0 引用数: 0 h-index: 0机构: Ist Sci San Raffaele, Div Regenerat Med Stem Cells & 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