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- [21] Inotersen improves quality of life and neuropathy in patients with hereditary transthyretin (hATTR) amyloidosis with polyneuropathy: results of the phase 3 study NEURO-TTREUROPEAN JOURNAL OF NEUROLOGY, 2018, 25 : 376 - 376Coelho, T.论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Porto, Porto, Portugal Ctr Hosp Porto, Porto, PortugalWang, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Orange, CA 92668 USA Ctr Hosp Porto, Porto, PortugalWaddington Cruz, M.论文数: 0 引用数: 0 h-index: 0机构: Fed Univ Rio de Janeiro Univ Hosp, Rio De Janeiro, Brazil Ctr Hosp Porto, Porto, PortugalPolydefkis, M.论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Baltimore, MD USA Ctr Hosp Porto, Porto, PortugalDyck, P.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Rochester, MN USA Ctr Hosp Porto, Porto, PortugalScheinberg, M.论文数: 0 引用数: 0 h-index: 0机构: Assoc Assistencia Crianca Deficiente, Sao Paulo, Brazil Ctr Hosp Porto, Porto, PortugalPlante-Bordeneuve, V.论文数: 0 引用数: 0 h-index: 0机构: CHU Henri Mondor, Creteil, France Ctr Hosp Porto, Porto, Portugal论文数: 引用数: h-index:机构:Barroso, F.论文数: 0 引用数: 0 h-index: 0机构: FLENI, Buenos Aires, DF, Argentina Ctr Hosp Porto, Porto, PortugalAdams, D.论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Sud, CHU Bicetre, Le Kremlin Bicetre, France Ctr Hosp Porto, Porto, Portugal论文数: 引用数: h-index:机构:Whelan, C.论文数: 0 引用数: 0 h-index: 0机构: UCL, Natl Amyloidosis Ctr, London, England Ctr Hosp Porto, Porto, PortugalMerlini, G.论文数: 0 引用数: 0 h-index: 0机构: Univ Pavia, IRCCS Policlin San Matteo, Amyloidosis Ctr, Pavia, Italy Ctr Hosp Porto, Porto, PortugalDrachman, B.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Philadelphia, PA 19104 USA Ctr Hosp Porto, Porto, PortugalHeitner, S.论文数: 0 引用数: 0 h-index: 0机构: Oregon Hlth & Sci Univ, Portland, OR 97201 USA Ctr Hosp Porto, Porto, PortugalConceicao, I.论文数: 0 引用数: 0 h-index: 0机构: CHLN, Hosp Santa Maria, Lisbon, Portugal UL, IMM Fac Med, Lisbon, Portugal Ctr Hosp Porto, Porto, PortugalSchmidt, H.论文数: 0 引用数: 0 h-index: 0机构: Univ Klinikum Munster, Munster, Germany Ctr Hosp Porto, Porto, PortugalVita, G.论文数: 0 引用数: 0 h-index: 0机构: Univ Messina, AOU Policlin G Martino, Messina, Italy Ctr Hosp Porto, Porto, PortugalGamez, J.论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Vall DHebron, Barcelona, Spain Ctr Hosp Porto, Porto, PortugalGane, E.论文数: 0 引用数: 0 h-index: 0机构: Auckland City Hosp, Auckland, New Zealand Ctr Hosp Porto, Porto, PortugalGorevic, P.论文数: 0 引用数: 0 h-index: 0机构: Mt Sinai Med Ctr, New York, NY 10029 USA Ctr Hosp Porto, Porto, PortugalSouza Bulle Oliveira, A.论文数: 0 引用数: 0 h-index: 0机构: Univ Fed Sao Paulo, Sao Paulo, Brazil Ctr Hosp Porto, Porto, PortugalMonia, B.论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut, Carlsbad, CA USA Ctr Hosp Porto, Porto, PortugalGertz, M.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Rochester, MN USA Ctr Hosp Porto, Porto, PortugalBenson, M.论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ Sch Med, Indianapolis, IN 46202 USA Ctr Hosp Porto, Porto, Portugal
- [22] BUDGET IMPACT OF INOTERSEN FOR THE TREATMENT OF STAGE I OR II POLYNEUROPATHY IN ADULT PATIENTS WITH HEREDITARY TRANSTHYRETIN AMYLOIDOSIS (hATTR) IN PUBLIC HEALTH MEXICOVALUE IN HEALTH, 2024, 27 (06) : S102 - S102Soto, H.论文数: 0 引用数: 0 h-index: 0机构: HS Estudios Farmacoecon SC CV, Mexico City, DF, Mexico HS Estudios Farmacoecon SC CV, Mexico City, DF, MexicoJuarez, Escobar Y.论文数: 0 引用数: 0 h-index: 0机构: HS Estudios Farmacoecon SC CV, Mexico City, DF, Mexico HS Estudios Farmacoecon SC CV, Mexico City, DF, MexicoColmenares, L.论文数: 0 引用数: 0 h-index: 0机构: PTC Therapeut, Bogota, Colombia HS Estudios Farmacoecon SC CV, Mexico City, DF, MexicoGuzman, Sotoi, I论文数: 0 引用数: 0 h-index: 0机构: HS Estudios Farmacoecon, Mexico City, DF, Mexico HS Estudios Farmacoecon SC CV, Mexico City, DF, Mexico
- [23] Inotersen Improves Norfolk Quality of Life-Diabetic Neuropathy Measures in Patients With Hereditary Transthyretin Amyloidosis with Polyneuropathy in the Phase 3 Study NEURO-TTRNEUROLOGY, 2018, 90Polydefkis, Michael J.论文数: 0 引用数: 0 h-index: 0机构: Johns Hopkins Univ, Baltimore, MD USA Johns Hopkins Univ, Baltimore, MD USACoelho, Teresa论文数: 0 引用数: 0 h-index: 0机构: Ctr Hosp Porto, Porto, Portugal Johns Hopkins Univ, Baltimore, MD USACruz, Marcia Waddington论文数: 0 引用数: 0 h-index: 0机构: Fed Univ Rio De Janeiro, Univ Hosp, Rio De Janeiro, Brazil Johns Hopkins Univ, Baltimore, MD USADyck, Peter J.论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Rochester, MN USA Johns Hopkins Univ, Baltimore, MD USAScheinberg, Morton论文数: 0 引用数: 0 h-index: 0机构: Assoc Assistencia Crianca Deficien, Sao Paulo, Brazil Johns Hopkins Univ, Baltimore, MD USAPlante-Bordeneuve, Violaine论文数: 0 引用数: 0 h-index: 0机构: CHU Henri Mondor, Creteil, France Johns Hopkins Univ, Baltimore, MD USA论文数: 引用数: h-index:机构:Barroso, Fabio论文数: 0 引用数: 0 h-index: 0机构: FLENI, Buenos Aires, DF, Argentina Johns Hopkins Univ, Baltimore, MD USAAdams, David论文数: 0 引用数: 0 h-index: 0机构: Univ Paris Sud, CHU Bicetre, Paris, France Johns Hopkins Univ, Baltimore, MD USA论文数: 引用数: h-index:机构:Whelan, Carol论文数: 0 引用数: 0 h-index: 0机构: Univ Coll London, Natl Amyloidosis Ctr, London, England Johns Hopkins Univ, Baltimore, MD USAMerlini, Giampaolo论文数: 0 引用数: 0 h-index: 0机构: IRCCS, Ctr Amiloidosi Fdn, Pavia, Italy Johns Hopkins Univ, Baltimore, MD USADrachman, Brian M.论文数: 0 引用数: 0 h-index: 0机构: Univ Penn, Philadelphia, PA 19104 USA Johns Hopkins Univ, Baltimore, MD USAHeitner, Stephen B.论文数: 0 引用数: 0 h-index: 0机构: Oregon Hlth & Sci Univ, Portland, OR 97201 USA Johns Hopkins Univ, Baltimore, MD USAConceicao, Isabel论文数: 0 引用数: 0 h-index: 0机构: Hosp Santa Maria, CHLN, Lisbon, Portugal Johns Hopkins Univ, Baltimore, MD USASchmidt, Hartmut论文数: 0 引用数: 0 h-index: 0机构: Univ Klinikum Munster, Munster, Germany Johns Hopkins Univ, Baltimore, MD USAVita, Giuseppe论文数: 0 引用数: 0 h-index: 0机构: Univ Messina, AOU Policlin G Martino, Messina, Italy Johns Hopkins Univ, Baltimore, MD USACampistol, Josep M.论文数: 0 引用数: 0 h-index: 0机构: Hosp Clin, Barcelona, Spain Johns Hopkins Univ, Baltimore, MD USAGamez, Josep论文数: 0 引用数: 0 h-index: 0机构: Hosp Univ Vall DHebron, Barcelona, Spain Johns Hopkins Univ, Baltimore, MD USAGane, Edward论文数: 0 引用数: 0 h-index: 0机构: Auckland City Hosp, Auckland, New Zealand Johns Hopkins Univ, Baltimore, MD USAGorevic, Peter论文数: 0 引用数: 0 h-index: 0机构: Mt Sinai Med Ctr, New York, NY 10029 USA Johns Hopkins Univ, Baltimore, MD USABulle Oliveira, Acary Souza论文数: 0 引用数: 0 h-index: 0机构: Univ Fed Sao Paulo, Sao Paulo, Brazil Johns Hopkins Univ, Baltimore, MD USAMonia, Brett P.论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut, Carlsbad, CA USA Johns Hopkins Univ, Baltimore, MD USAHughes, Steven G.论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut, Carlsbad, CA USA Johns Hopkins Univ, Baltimore, MD USAKwoh, Jesse论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut, Carlsbad, CA USA Johns Hopkins Univ, Baltimore, MD USAMcEvoy, Bradley W.论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut, Carlsbad, CA USA Johns Hopkins Univ, Baltimore, MD USABaker, Brenda F.论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut, Carlsbad, CA USA Johns Hopkins Univ, Baltimore, MD USAAckermann, Elizabeth J.论文数: 0 引用数: 0 h-index: 0机构: Ionis Pharmaceut, Carlsbad, CA USA Johns Hopkins Univ, Baltimore, MD USAGertz, Morie论文数: 0 引用数: 0 h-index: 0机构: Mayo Clin, Rochester, MN USA Johns Hopkins Univ, Baltimore, MD USABenson, Merrill D.论文数: 0 引用数: 0 h-index: 0机构: Indiana Univ Sch Med, Indianapolis, IN 46202 USA Johns Hopkins Univ, Baltimore, MD USAWang, Annabel K.论文数: 0 引用数: 0 h-index: 0机构: Univ Calif Irvine, Irvine, CA USA Johns Hopkins Univ, Baltimore, MD USA