Intraosseous Delivery of Lentiviral Virus Acts as a Therapeutic Strategy for In Vivo Gene Therapy of Hemophilia

被引:0
|
作者
Wang, Xuefeng [1 ]
Sign, Swati [1 ]
Kiem, Hans-Peter [2 ]
Rawlings, David J. [1 ]
Miao, Carol H. [1 ]
机构
[1] Seattle Childrens Res Inst, Seattle, WA USA
[2] Fred Hutchinson Canc Res Ctr, 1124 Columbia St, Seattle, WA 98104 USA
关键词
D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
601
引用
收藏
页码:278 / 278
页数:1
相关论文
共 50 条
  • [1] Hemophilia A gene therapy via intraosseous delivery of factor VIII-lentiviral vectors
    Miao C.H.
    Thrombosis Journal, 14 (Suppl 1)
  • [2] Evaluation of the Efficacy and Safety of Intraosseous Delivery of Platelet-Specific Factor VIII-Lentiviral Vectors as an In Vivo Gene Therapy for Hemophilia in Humanized NSG Mice
    Joo, Julia H.
    Wang, Xuefeng
    Singh, Swati
    Li, Chong
    Adair, Jennifer E.
    Kiem, Hans-Peter
    Rawlings, David J.
    Miao, Carol H.
    MOLECULAR THERAPY, 2019, 27 (04) : 323 - 324
  • [3] Lentiviral vector for hemophilia gene therapy
    Herzog, RW
    BLOOD, 2004, 103 (10) : 3609 - 3610
  • [4] In vivo gene delivery by lentiviral vectors
    Naldini, L
    THROMBOSIS AND HAEMOSTASIS, 1999, 82 (02) : 552 - 554
  • [5] Enhancing Factor VIII Expression in Platelets of Hemophilia A Mice Following Intraosseous Delivery of Lentiviral Vectors
    Wang, Xuefeng
    Lyle, Meghan J.
    Fu, Richard
    Miao, Carol H.
    MOLECULAR THERAPY, 2015, 23 : S96 - S96
  • [6] Intraosseous Delivery of Lentiviral Vectors Targeting Factor VIII Expression in Platelets Corrects Murine Hemophilia A
    Wang, Xuefeng
    Shin, Simon C.
    Chiang, Andy F. J.
    Khan, Iram
    Pan, Dao
    Rawlings, David J.
    Miao, Carol H.
    MOLECULAR THERAPY, 2015, 23 (04) : 617 - 626
  • [7] Development and characterization of lentiviral vectors for hemophilia gene therapy
    Thorrez, L
    Maris, M
    Miao, C
    Van Rooijen, N
    Collen, D
    Chuah, M
    VandenDriessche, T
    MOLECULAR THERAPY, 2004, 9 : S158 - S159
  • [8] In vivo gene delivery to synovium by lentiviral vectors
    Gouze, E
    Pawliuk, R
    Pilapil, C
    Gouze, JN
    Fleet, C
    Palmer, GD
    Evans, CH
    Leboulch, P
    Ghivizzani, SC
    MOLECULAR THERAPY, 2002, 5 (04) : 397 - 404
  • [9] A Novel Strategy of Lung-Specific Gene Therapy for the Treatment of Hemophilia A via Intranasal Delivery of Lentiviral Vectors Encoding Factor VIII
    Li, Chong
    Chen, Chun-Yu
    Miao, Carol
    MOLECULAR THERAPY, 2019, 27 (04) : 275 - 276
  • [10] A Novel Strategy for Platelet-Specific Gene Therapy for the Treatment of Hemophilia A via Intranasal Delivery Lentiviral Vectors Containing Factor VIII
    Rementer, Cameron W.
    Li, Chong
    Chen, Chun-Yu
    Cai, Xiaohe
    Miao, Carol H.
    MOLECULAR THERAPY, 2022, 30 (04) : 333 - 333