A Systematic Literature Review of Clinical and Economic Outcomes for Patients with Paroxysmal Nocturnal Hemoglobinuria in Clinical Trials and Real-World Settings

被引:2
|
作者
Waheed, Anem [1 ]
Kaufhold, Samantha [2 ]
Liu, Che-Rung [2 ]
Lei, Jiali [2 ]
Nellesen, Dave [3 ]
Geevarghese, Anumaxine Lincy [4 ]
Yen, Glorian P. [4 ]
机构
[1] Harvard Med Sch, Massachusetts Gen Hosp, MGH Canc Ctr, Boston, MA USA
[2] Anal Grp Inc, Menlo Pk, CA USA
[3] Anal Grp Inc, San Francisco, CA USA
[4] Novartis Pharmaceut, E Hanover, NJ USA
关键词
D O I
10.1182/blood-2022-167531
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:11451 / 11452
页数:2
相关论文
共 50 条
  • [41] Clinical and economic outcomes in a real-world population of patients with elevated triglyceride levels
    Toth, Peter P.
    Grabner, Michael
    Ramey, Nadia
    Higuchi, Keiko
    [J]. ATHEROSCLEROSIS, 2014, 237 (02) : 790 - 797
  • [42] Impact of Natalizumab on Economic and Clinical Outcomes in MS Patients in the Real-World Setting
    Cai, Qian
    Tan, Hiangkiat
    Agarwal, Sonalee
    Kamat, Siddhesh
    [J]. NEUROLOGY, 2010, 74 (09) : A65 - A65
  • [43] Clinical and epidemiological features of paroxysmal cold hemoglobinuria: a systematic review
    Jacobs, Jeremy W.
    Villalba, Cristina A. Figueroa
    Booth, Garrett S.
    Woo, Jennifer S.
    Stephens, Laura D.
    Adkins, Brian D.
    [J]. BLOOD ADVANCES, 2023, 7 (11) : 2520 - 2527
  • [44] Clinical trials and "real-world" medicine
    Simes, RJ
    [J]. MEDICAL JOURNAL OF AUSTRALIA, 2002, 177 (08) : 410 - 411
  • [45] Effectiveness of ocriplasmin in real-world settings: A systematic literature review, meta-analysis, and comparison with randomized trials
    Khanani, Arshad M.
    Constantine, Ryan N.
    Blot, Koenraad H.
    Lescrauwaet, Benedicte
    Szurman, Peter
    [J]. ACTA OPHTHALMOLOGICA, 2021, 99 (06) : E823 - E836
  • [46] Clinical management of paroxysmal nocturnal hemoglobinuria in pregnancy: A case report and updated review
    Fieni, Stefania
    Bonfanti, Laura
    Gramellini, Dandolo
    Benassi, Luigi
    Delsignore, Roberto
    [J]. OBSTETRICAL & GYNECOLOGICAL SURVEY, 2006, 61 (09) : 593 - 601
  • [47] The Real-World Characteristics and Outcomes of Newly Diagnosed Myeloma Patients Ineligible for Clinical Trials
    Fiala, Mark
    Dukeman, James
    Stockerl-Goldstein, Keith
    Tomasson, Michael
    Wildes, Tanya
    Vij, Ravi
    [J]. CLINICAL LYMPHOMA MYELOMA & LEUKEMIA, 2017, 17 (01): : E55 - E56
  • [48] The Real-World Characteristics and Outcomes of Newly Diagnosed Myeloma Patients Ineligible for Clinical Trials
    Fiala, Mark A.
    Dukeman, James
    Stockerl-Goldstein, Keith
    Tomasson, Michael H.
    Wildes, Tanya M.
    Vij, Ravi
    [J]. BLOOD, 2016, 128 (22)
  • [49] REAL-WORLD OUTCOMES VERSUS CLINICAL TRIALS RESULTS WITH DIPEPTIDYL PEPTIDASE-4 INHIBITORS: A SYSTEMATIC REVIEW PROTOCOL
    Batel-Marques, F.
    Pereira, D.
    Mendes, D.
    Alves, C.
    Penedones, A.
    [J]. DIABETES TECHNOLOGY & THERAPEUTICS, 2020, 22 : A104 - A105
  • [50] Clinical course and disease burden in patients with paroxysmal nocturnal hemoglobinuria by hemolytic status
    Yenerel, Mustafa N.
    Muus, Petra
    Wilson, Amanda
    Szer, Jeff
    [J]. BLOOD CELLS MOLECULES AND DISEASES, 2017, 65 : 29 - 34