EFFICACY AND SAFETY OF PXT3003 IN PATIENTS WITH CHARCOT-MARIE-TOOTH DISEASE TYPE 1A: RESULTS OF PLEO-CHARCOT-MARIE-TOOTH: AN INTERNATIONAL PIVOTAL PHASE III TRIAL

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作者：
Thomas, Florian
Boutalbi, Youcef
Fitoussi, Serge
Rinaudo, Philippe
Bertrand, Viviane
Hajj, Rodolphe
Nabirotchkin, Serguei
Cohen, Daniel
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MUSCLE & NERVE | 2019年 / 60卷
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R74 [神经病学与精神病学];
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92
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页码：S46 / S46
页数：1
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