ZFN-Mediated Minigene or Dinucleotide Gene Correction of p47phox Deficient Autosomal Recessive Chronic Granulomatous Disease iPSC to Generate Oxidase Functional Neutrophils

被引：0

作者：

Merling, Randall K. ^{[1
]}

De Ravin, Suk See ^{[1
]}

Sweeney, Colin L. ^{[1
]}

Kuhns, Douglas B. ^{[2
]}

Di Pasquale, Giovanni ^{[3
]}

Chiorini, John A. ^{[3
]}

Malech, Harry L. ^{[1
]}

机构：

[1] NIAID, Lab Host Def, NIH, Bethesda, MD 20892 USA

[2] NIAID, Neutrophil Monitoring Lab, Appl Dev Res Directorate, Leidos Biomed Res Inc,NIH, Frederick, MD USA

[3] Natl Inst Dent & Craniofacial Res, Adeno Associated Virus Sect, NIH, Bethesda, MD USA

来源：

MOLECULAR THERAPY | 2015年 / 23卷

关键词：

D O I：

10.1016/S1525-0016(16)33941-7

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

332

引用

页码：S133 / S133

页数：1

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