ZFN-Mediated Minigene or Dinucleotide Gene Correction of p47phox Deficient Autosomal Recessive Chronic Granulomatous Disease iPSC to Generate Oxidase Functional Neutrophils

被引：0
|
作者：
Merling, Randall K. [1 ]
De Ravin, Suk See [1 ]
Sweeney, Colin L. [1 ]
Kuhns, Douglas B. [2 ]
Di Pasquale, Giovanni [3 ]
Chiorini, John A. [3 ]
Malech, Harry L. [1 ]
机构：
[1] NIAID, Lab Host Def, NIH, Bethesda, MD 20892 USA
[2] NIAID, Neutrophil Monitoring Lab, Appl Dev Res Directorate, Leidos Biomed Res Inc,NIH, Frederick, MD USA
[3] Natl Inst Dent & Craniofacial Res, Adeno Associated Virus Sect, NIH, Bethesda, MD USA
来源：
MOLECULAR THERAPY | 2015年 / 23卷
关键词：
D O I：
10.1016/S1525-0016(16)33941-7
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
332
引用
收藏
页码：S133 / S133
页数：1
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