AAV liver gene therapy-mediated inhibition of FGF23 signaling as a therapeutic strategy for X-linked hypophosphatemia

被引：0
|
作者：
Zhukouskaya, Volha [1 ,2 ]
Jauze, Louisa [1 ,2 ,3 ]
Charles, Severine [1 ,2 ]
Leborgne, Christian [1 ,2 ]
Hilliquin, Stephane [4 ]
Sadoine, Jeremy [5 ]
Slimani, Lotfi [5 ]
Baroukh, Brigitte [5 ]
van Wittenberghe, Laetitia [2 ]
Daniele, Natalie [2 ]
Rajas, Fabienne [3 ]
Linglart, Agnes [6 ,7 ,8 ]
Mingozzi, Federico [1 ,2 ]
Chaussain, Catherine [5 ,9 ,10 ,11 ]
Bardet, Claire [5 ]
Ronzitti, Giuseppe [1 ,2 ]
机构：
[1] Univ Paris Saclay, Univ Evry, Integrare Res Unit UMR S951, INSERM, Evry, France
[2] Genethon, Evry, France
[3] Inst Natl Sante & Rech Med, U1213, Lyon, France
[4] Univ Paris, Cochin Hosp, Dept Rheumatol, Paris, France
[5] Univ Paris, Lab Orofacial Pathol Imaging & Biotherapies, URP2496 & FHU DDS Net, Dent Sch & Plateforme Imagerie Vivant PIV, Montrouge, France
[6] Bicetre Paris Saclay Hosp, AP HP, Dept Endocrinol & Diabetol Children, Le Kremlin Bicetre, France
[7] AP HP, Bicetre Paris Saclay Hosp, Dept Adolescent Med, Le Kremlin Bicetre, France
[8] Paris Saclay Univ, Fac Med, Le Kremlin Bicetre, France
[9] Univ Paris, AP HP, Hosp Bretonneau, Dept Odontol Rare Disorders, Paris, France
[10] Univ Paris, UR2496, Paris, France
[11] Univ Paris, Paris, France
来源：
HORMONE RESEARCH IN PAEDIATRICS | 2021年 / 94卷 / SUPPL 1期
关键词：
D O I：
暂无
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
P1-58
引用
收藏
页码：97 / 97
页数：1
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