Comprehensive Evaluation of a Barcoded AAV Library in Non-Human Primate Central Nervous System

被引：0
|
作者：
Kondratov, O. [1 ]
Kondratova, L. [1 ]
Mandel, R. J. [2 ]
Gamlin, P. [3 ]
Bell, R. [4 ]
Rabinowitz, J. [4 ]
Rodriquez, E. [5 ]
Zolotukhin, S. [1 ]
机构：
[1] Univ Florida, Dept Pediat, COM, Gainesville, FL USA
[2] Univ Florida, Dept Neurosci, COM, Gainesville, FL 32610 USA
[3] Univ Alabama Birmingham, Dept Ophthalmol & Visual Sci, Birmingham, AL USA
[4] Pfizer Inc, Rare Dis Res Unit, Cambridge, MA USA
[5] Lacerta Therapeut Inc, Alachua, FL USA
来源：
MOLECULAR THERAPY | 2020年 / 28卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
93
引用
收藏
页码：48 / 48
页数：1
相关论文
共 50 条
  • [21] Axonal transport of a modified AAV2 in the non-human primate brain
    Ohno, K.
    Stanek, L. M.
    Naidoo, J.
    Trewman, S.
    Samaranch, L.
    Hadaczek, P.
    O'Riordan, C.
    Sullivan, J.
    San Sebastian, W.
    Bringas, J. R.
    Snieckus, C.
    Mahmoodi, A.
    Mahmoodi, A.
    Forsayeth, J.
    Shihabuddin, L. S.
    Bankiewicz, K. S.
    HUMAN GENE THERAPY, 2018, 29 (12) : A153 - A153
  • [22] Non-Human Primate Pharmacology of AAV Gene Therapy Vectors for Hereditary Angioedema
    Fleming, James
    Towle, Theresa A.
    Narula, Jatin
    Khatri, Arpana
    Cheng, Ting-Wen
    Xuong, Kevin
    Vinh Le
    Palandra, Joseph
    Souza, David W.
    Al-Sowaimel, Lujain
    Bazile, Marla
    Nisraiyya, Sagar Patel
    Srnka, Alexandra
    Zhou, Hongru
    Aliagan, Abdulhafiz Imam
    Choudhury, Sumana
    Manibog, Kristine
    Murakami, Naoko
    Sapashnik, Diana
    Zaraspe, Kimberly
    Tabet, Ricardos
    Keyes, Lisa R.
    Rao-Dayton, Sheila
    Sievers, Annette
    Brodfuehrer, Joanne
    Lopes, Sarah H.
    Bolt, Michael W.
    Somanathan, Sury
    Pregel, Marko J.
    MOLECULAR THERAPY, 2023, 31 (04) : 527 - 528
  • [23] Evaluation of Dose and Safety of AAV7m8 and AAV8BP2 in the Non-Human Primate Retina
    Ramachandran, Pavitra S.
    Lee, Vivian
    Wei, Zhangyong
    Song, Ji Yun
    Casal, Giulia
    Cronin, Therese
    Willett, Keirnan
    Huckfeldt, Rachel
    Morgan, Jessica I. W.
    Aleman, Tomas S.
    Maguire, Albert M.
    Bennett, Jean
    HUMAN GENE THERAPY, 2017, 28 (02) : 154 - 167
  • [24] Evaluation of AAV Variants for Transgene Expression and Distribution in Rabbits and Non-Human Primate Eyes Following Intravitreal Delivery
    Iglesias, Bibiana Veronica
    Woodburn, Kathryn W.
    Cao, Jingtai
    Wiegand, Stanley J.
    Keravala, Annahita
    Romano, Carmelo
    Gasmi, Mehdi
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2016, 57 (12)
  • [25] Intravenous Administration of a Barcoded and Pooled AAV Library for the Comprehensive Characterization and Comparison of Capsid Tropisms
    Giles, April R.
    Yost, Samantha A.
    Firnberg, Elad
    Egley, Jenny M.
    Janczura, Karolina J.
    Henry, William M.
    Liu, Ye
    Karumuthil-Melethil, Subha
    Mercer, Andrew C.
    MOLECULAR THERAPY, 2021, 29 (04) : 97 - 97
  • [26] Evaluation of a Human Neurovascular Model to Complement a Parallel Non-Human Primate Selection for Blood Brain Barrier Penetrant AAV Capsids
    Tiffany, Matthew R.
    Frias, Stephanye
    Goodwin, Alicia
    Ward, Alex
    Tran, Hung
    Prawdzik, Gregg
    Kennard, Kenneth
    Ojala, David S.
    Zeitler, Bryan J.
    Pooler, Amy M.
    MOLECULAR THERAPY, 2022, 30 (04) : 425 - 425
  • [27] Injections of AAV Vectors for Optogenetics in Anesthetized and Awake Behaving Non-Human Primate Brain
    Kojima, Yoshiko
    Ting, Jonathan T.
    Soetedjo, Robijanto
    Gibson, Shane D.
    Horwitz, Gregory D.
    JOVE-JOURNAL OF VISUALIZED EXPERIMENTS, 2021, (174):
  • [28] Simultaneous Pharmacokinetic Profiling of Multiple AAV Serotypes and Mutants in a Non-Human Primate by AAV Barcode-Seq
    Adachi, Kei
    Kawano, Yasuhiro
    Dissen, Gregory A.
    Ojeda, Sergio R.
    Nakai, Hiroyuki
    MOLECULAR THERAPY, 2013, 21 : S31 - S32
  • [29] NON-HUMAN PRIMATE CULTURE
    WASHBURN, SL
    BENEDICT, B
    MAN, 1979, 14 (01): : 163 - 164
  • [30] Comprehensive Evaluation of an AAV Library in the Mice and Nonhuman Primate Ocular Tissues Following Intravitreal Delivery
    Lee, Wei-Hua
    McDougald, Devin S.
    Giles, April R.
    Firnberg, Elad
    Egley, Jenny M.
    Yost, Samantha A.
    Janczura, Karolina J.
    Glenn, Justin
    Henry, William M.
    Elliott, Kirk
    Qian, Randolph
    Qiao, Chunping
    Smith, Jared
    Liu, Ye
    Bruder, Joseph
    Danos, Olivier
    Karumuthil-Melethil, Subha
    Mercer, Andrew
    Wang, Xu
    MOLECULAR THERAPY, 2021, 29 (04) : 276 - 276
12345