Immune Responses to Adeno-Associated Virus-Mediated CRISPR Therapy

被引:1
|
作者
Keeler, Allison M. [1 ,2 ,3 ]
机构
[1] Univ Massachusetts, Chan Med Sch, Horae Gene Therapy Ctr, Worcester, MA 01605 USA
[2] Univ Massachusetts, Chan Med Sch, Dept Pediat, Worcester, MA 01605 USA
[3] Univ Massachusetts, Chan Med Sch, NeuroNexus Inst, Worcester, MA 01605 USA
关键词
T-CELL RESPONSES; ALIPOGENE TIPARVOVEC AAV1-LPLS447X; CLINICAL-TRIAL; ALPHA-GLUCOSIDASE; GENE-THERAPY; VECTOR; DYSTROPHY; SAFETY;
D O I
10.1089/hum.2021.29193.amk
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
引用
收藏
页码:1430 / 1432
页数:3
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