Immune Responses to Adeno-Associated Virus-Mediated CRISPR Therapy

被引:1
|
作者
Keeler, Allison M. [1 ,2 ,3 ]
机构
[1] Univ Massachusetts, Chan Med Sch, Horae Gene Therapy Ctr, Worcester, MA 01605 USA
[2] Univ Massachusetts, Chan Med Sch, Dept Pediat, Worcester, MA 01605 USA
[3] Univ Massachusetts, Chan Med Sch, NeuroNexus Inst, Worcester, MA 01605 USA
关键词
T-CELL RESPONSES; ALIPOGENE TIPARVOVEC AAV1-LPLS447X; CLINICAL-TRIAL; ALPHA-GLUCOSIDASE; GENE-THERAPY; VECTOR; DYSTROPHY; SAFETY;
D O I
10.1089/hum.2021.29193.amk
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
引用
收藏
页码:1430 / 1432
页数:3
相关论文
共 50 条
  • [1] Adeno-Associated Virus-Mediated Gene Therapy
    Zaman, Hassan
    Khan, Aakif
    Khan, Khalid
    Toheed, Shazma
    Abdullah, Muhammad
    Zeeshan, Hafiz Muhammad
    Hameed, Abdul
    Umar, Muhammad
    Shahid, Muhammad
    Malik, Kausar
    Afzal, Samia
    CRITICAL REVIEWS IN EUKARYOTIC GENE EXPRESSION, 2023, 33 (06): : 87 - 100
  • [2] Adeno-associated virus-mediated gene therapy for cancer
    Collins, Sara
    Harrison, P. T.
    Scallan, M. F.
    O'Sullivan, Gerald C.
    Tangney, Mark
    HUMAN GENE THERAPY, 2007, 18 (10) : 999 - 999
  • [3] Adeno-Associated Virus-Mediated Gene Therapy for Metabolic Myopathy
    Mah, Cathryn S.
    Soustek, Meghan S.
    Todd, A. Gary
    McCall, Angela
    Smith, Barbara K.
    Corti, Manuela
    Falk, Darin J.
    Byrne, Barry J.
    HUMAN GENE THERAPY, 2013, 24 (11) : 928 - 936
  • [4] Adeno-associated virus-mediated gene therapy in cardiovascular disease
    Hammoudi, Nadjib
    Ishikawa, Kiyotake
    Hajjar, Roger J.
    CURRENT OPINION IN CARDIOLOGY, 2015, 30 (03) : 228 - 234
  • [5] Adeno-Associated Virus-Mediated Delivery of CRISPR for Cardiac Gene Editing in Mice
    Xu, Li
    Gao, Yandi
    Lau, Yeh Siang
    Han, Renzhi
    JOVE-JOURNAL OF VISUALIZED EXPERIMENTS, 2018, (138):
  • [6] Adeno-associated virus-mediated gene delivery
    Snyder, RO
    JOURNAL OF GENE MEDICINE, 1999, 1 (03): : 166 - 175
  • [7] Adeno-associated virus-mediated gene transfer
    Srivastava, Arun
    JOURNAL OF CELLULAR BIOCHEMISTRY, 2008, 105 (01) : 17 - 24
  • [8] Potential innate immune responses to adeno-associated virus mediated gene therapy
    Bucher, K.
    Rodriguez-Bocanegra, E.
    Dauletbekov, D.
    Bonillo, M.
    Pfromm, J. K.
    Fischer, M. D.
    HUMAN GENE THERAPY, 2019, 30 (11) : A117 - A117
  • [9] Translational Aspects of Adeno-Associated Virus-Mediated Cardiac Gene Therapy
    Ziegler, Tilman
    Ishikawa, Kiyotake
    Hinkel, Rabea
    Kupatt, Christian
    HUMAN GENE THERAPY, 2018, 29 (12) : 1341 - 1351
  • [10] Adeno-associated virus-mediated cancer gene therapy: Current status
    Luo, Jingfeng
    Luo, Yuxuan
    Sun, Jihong
    Zhou, Yurong
    Zhang, Yajing
    Yang, Xiaoming
    CANCER LETTERS, 2015, 356 (02) : 347 - 356