Five-Year Post-Injection Results of the Phase 3 Trial of Voretigene Neparvovec-rzyl in Biallelic RPE65 Mutation-Associated Inherited Retinal Disease

被引：0
|
作者：
Bennett, Jean [1 ,2 ]
Russell, Stephen R. [3 ]
High, Katherine A. [4 ]
Drack, Arlene V. [3 ]
Yu, Zi-Fan [5 ]
Chung, Daniel C. [4 ]
Reape, Kathy [4 ]
Maguire, Albert M. [1 ,2 ]
机构：
[1] Childrens Hosp Philadelphia, Ophthalmol, Philadelphia, PA 19104 USA
[2] Univ Penn, Perelman Sch Med, Ophthalmol, Philadelphia, PA 19104 USA
[3] Univ Iowa, Iowa City, IA USA
[4] Spark Therapeut Inc, Philadelphia, PA USA
[5] Stat Collaborat Inc, Washington, DC USA
来源：
INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE | 2021年 / 62卷 / 08期
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D O I：
暂无
中图分类号：
R77 [眼科学];
学科分类号：
100212 ;
摘要：
3540
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页数：3
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