Lentiviral Gene Therapy for p47phox Deficient Chronic Granulomatous Disease: One Step Closer to the Clinic

被引：0
|
作者：
Schejtman, Andrea [1 ]
Vetharoy, Winston [1 ]
Choi, Uimook [2 ]
Narda, Theobald [2 ]
Rothe, Michael [3 ]
Rivat, Christine [1 ]
Piras, Giuseppa [1 ]
Schambach, Axel [3 ,4 ]
Malech, Harry L. [4 ]
Thrasher, Adrian J. [1 ]
Santilli, Giorgia [1 ]
机构：
[1] UCL Great Ormond St Inst Child Hlth, London, England
[2] NIAID, Lab Clin Immunol & Microbiol, NIH, Bethesda, MA USA
[3] Hannover Med Sch, Inst Expt Hematol, Hannover, Germany
[4] Harvard Med Sch, Boston Childrens Hosp, Div Hematol Oncol, Boston, MA 02115 USA
来源：
MOLECULAR THERAPY | 2020年 / 28卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
910
引用
收藏
页码：394 / 395
页数：2
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