Lentiviral Gene Therapy for p47phox Deficient Chronic Granulomatous Disease: One Step Closer to the Clinic

被引：0

作者：

Schejtman, Andrea ^{[1
]}

Vetharoy, Winston ^{[1
]}

Choi, Uimook ^{[2
]}

Narda, Theobald ^{[2
]}

Rothe, Michael ^{[3
]}

Rivat, Christine ^{[1
]}

Piras, Giuseppa ^{[1
]}

Schambach, Axel ^{[3
,4
]}

Malech, Harry L. ^{[4
]}

Thrasher, Adrian J. ^{[1
]}

Santilli, Giorgia ^{[1
]}

机构：

[1] UCL Great Ormond St Inst Child Hlth, London, England

[2] NIAID, Lab Clin Immunol & Microbiol, NIH, Bethesda, MA USA

[3] Hannover Med Sch, Inst Expt Hematol, Hannover, Germany

[4] Harvard Med Sch, Boston Childrens Hosp, Div Hematol Oncol, Boston, MA 02115 USA

来源：

MOLECULAR THERAPY | 2020年 / 28卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

910

引用

页码：394 / 395

页数：2

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