Optimization of hammerhead ribozymes targeted against human P23H rod opsin RNA associated with autosomal dominant retinitis pigmentosa (ADRP)

被引：0
|
作者：
Fritz, JJ [1 ]
Lewin, AS [1 ]
Hauswirth, WW [1 ]
机构：
[1] Univ Florida, Gainesville, FL 32610 USA
来源：
FASEB JOURNAL | 2001年 / 15卷 / 05期
关键词：
D O I：
暂无
中图分类号：
Q5 [生物化学]; Q7 [分子生物学];
学科分类号：
071010 ; 081704 ;
摘要：
引用
收藏
页码：A881 / A881
页数：1
相关论文
共 45 条
  • [41] Prevalence Estimates and Genetic Diversity for Autosomal Dominant Retinitis Pigmentosa Due to RHO , c.68C > A (p.P23H) Variant
    Leenders, Matthijs
    Gaastra, Mathijs
    Jayagopal, Ash
    Malone, Karen E.
    AMERICAN JOURNAL OF OPHTHALMOLOGY, 2024, 268 : 340 - 347
  • [42] The Antiapoptotic TUDCA Protects Against Mitochondrial Dysfunction, Glial Cell Changes and Loss of the Capillary Network in the Transgenic Rat Model of Retinitis Pigmentosa P23H
    Fernandez-Sanchez, L.
    Esquiva, G.
    Pinilla, I.
    Martin-Nieto, I.
    Cuenca, N.
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2010, 51 (13)
  • [43] Activation of Sigma1 Receptor (Sig1R) improves retinal architecture & visual acuity in the RhoP23H/+ mouse model of autosomal dominant retinitis pigmentosa (adRP)
    Barwick, Shannon
    Xiao, Haiyan
    Wang, Jing
    Smith, Sylvia B.
    INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2020, 61 (07)
  • [44] Treatment of autosomal dominant retinitis pigmentosa caused by RHO-P23H mutation with high-fidelity Cas13X in mice
    Yan, Zixiang
    Yao, Yuqin
    Li, Luyao
    Cai, Lingqiong
    Zhang, Haiwei
    Zhang, Shenghai
    Xiao, Qingquan
    Wang, Xing
    Zuo, Erwei
    Xu, Chunlong
    Wu, Jihong
    Yang, Hui
    MOLECULAR THERAPY NUCLEIC ACIDS, 2023, 33 : 750 - 761
  • [45] CRISPR/Cas9 gene editing for retinitis pigmentosa (RP): use of a selective guide discriminating the mutant dominant P23H from the wild-type rhodopsin (Rho) allele.
    Giannelli, G.
    Luoni, M.
    Massimino, L.
    Broccoli, V.
    HUMAN GENE THERAPY, 2016, 27 (11) : A119 - A119
12345