AAV6.2: An efficient and safe gene therapy clinical candidate for the treatment of cystic fibrosis airway disease

被引：0
|
作者：
Limberis, M. [1 ]
Vandenberghe, L. H. [1 ]
Zhang, L. [2 ]
Pickles, R. J. [2 ]
Wilson, J. M. [1 ]
机构：
[1] Univ Penn, Dept Pathol & Lab Med, Philadelphia, PA 19104 USA
[2] Univ N Carolina, Csyt Fibrosis Pulm Res & Treatment Ctr, Chapel Hill, NC 27515 USA
来源：
PEDIATRIC PULMONOLOGY | 2007年
关键词：
D O I：
暂无
中图分类号：
R72 [儿科学];
学科分类号：
100202 ;
摘要：
273
引用
收藏
页码：298 / 298
页数：1
相关论文
共 50 条
  • [1] A novel AAV vector for the treatment of cystic fibrosis airway disease
    Limberis, M
    Gao, GP
    Weiner, DJ
    Wang, LL
    Bell, P
    Wilson, JM
    MOLECULAR THERAPY, 2004, 9 : S262 - S263
  • [2] Gene therapy for cystic fibrosis airway disease - Is clinical success imminent?
    Anson, Donald S.
    Smith, Gregory J.
    Parsons, David W.
    CURRENT GENE THERAPY, 2006, 6 (02) : 161 - 179
  • [3] Perspectives on gene therapy for cystic fibrosis airway disease
    Bigger, B
    Coutelle, C
    BIODRUGS, 2001, 15 (09) : 615 - 634
  • [4] Perspectives on Gene Therapy for Cystic Fibrosis Airway Disease
    Brian Bigger
    Charles Coutelle
    BioDrugs, 2001, 15 : 615 - 534
  • [5] Airway gene therapy and cystic fibrosis
    Parsons, DW
    JOURNAL OF PAEDIATRICS AND CHILD HEALTH, 2005, 41 (03) : 94 - 96
  • [6] Roadmap for an early gene therapy for cystic fibrosis airway disease
    Carlon, Marianne S.
    Vidovic, Dragana
    Birket, Susan
    PRENATAL DIAGNOSIS, 2017, 37 (12) : 1181 - 1190
  • [7] Perceptions of airway gene therapy for cystic fibrosis
    Donnelley, Martin
    Parsons, David
    Prichard, Ivanka
    EXPERT OPINION ON BIOLOGICAL THERAPY, 2023, 23 (01) : 103 - 113
  • [8] Cellular barriers to efficient AAV-mediated CFTR gene delivery to polarized airway epithelial cells for the treatment of cystic fibrosis
    Bartlett, JS
    PEDIATRIC RESEARCH, 2000, 47 (04) : 238A - 238A
  • [9] Gene therapy for the treatment of cystic fibrosis
    Burney, Tabinda J.
    Davies, Jane C.
    APPLICATION OF CLINICAL GENETICS, 2012, 5 : 29 - 36
  • [10] Functional Cystic Fibrosis Transmembrane Conductance Regulator Expression in Cystic Fibrosis Airway Epithelial Cells by AAV6.2-Mediated Segmental Trans-Splicing
    Song, Yuhu
    Lou, Howard H.
    Boyer, Julie L.
    Limberis, Maria P.
    Vandenberghe, Luk H.
    Hackett, Neil R.
    Leopold, Philip L.
    Wilson, James M.
    Crystal, Ronald G.
    HUMAN GENE THERAPY, 2009, 20 (03) : 267 - 281
12345