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- [32] Intrathecal Gene Therapy for Giant Axonal Neuropathy NEW ENGLAND JOURNAL OF MEDICINE, 2024, 390 (12): : 1092 - 1104
- [34] Sonic Hedgehog repression underlies gigaxonin mutation-induced motor deficits in giant axonal neuropathy JOURNAL OF CLINICAL INVESTIGATION, 2019, 129 (12): : 5312 - 5326