RESTORATION OF CFTR FUNCTION BY ANTISENSE OLIGONUCLEOTIDE SPLICING MODULATION

被引：0
|
作者：
Oren, Y. [1 ,2 ]
Tur-Sinai, Irony M. [1 ]
Ozeri-Galai, E. [1 ,2 ]
Avizur, O. [1 ,2 ]
Mutyam, V [3 ]
Wilton, S. [4 ]
Rowe, S. M. [3 ]
Kerem, B. [1 ]
机构：
[1] Hebrew Univ Jerusalem, Genet, Jerusalem, Israel
[2] SpliSense, Jerusalem, Israel
[3] Univ Alabama Birmingham, Birmingham, AL USA
[4] Univ Western Australia, Ctr Neuromuscular & Neurol Disorders, Crawley, WA, Australia
来源：
PEDIATRIC PULMONOLOGY | 2017年 / 52卷
关键词：
D O I：
暂无
中图分类号：
R72 [儿科学];
学科分类号：
100202 ;
摘要：
261
引用
收藏
页码：S313 / S313
页数：1
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