Short-term effect of oral treatment with miglustat in type 1 Gaucher disease.

被引：0
|
作者：
Giraldo, P
Alonso, D
Acedo, M
Franco, R
Barez, A
Corrales, A
Serrano, D
Roldan, V
Latre, P
Alfonso, P
Pocovi, M
机构：
[1] Miguel Servet Univ Hosp, Zaragoza, Spain
[2] Virgen Rocio Univ Hosp, Seville, Spain
[3] Vega Baja Hosp, Alicante, Spain
[4] Punta Europa Univ Hosp, Cadiz, Spain
[5] Ntra Sra Sansoles Hosp, Avila, Spain
[6] Virgen Concha Hosp, Zamora, Spain
[7] Gen Hosp, Alicante, Spain
[8] San Vicente Hosp, Alicante, Spain
[9] Spanish Fdn Study & Therapy Gaucher Dis, FEETEG, Zaragoza, Spain
[10] Inst Aragones Hlth Sci, I & CS, Zaragoza, Spain
[11] Univ Zaragoza, Zaragoza, Spain
来源：
BLOOD | 2005年 / 106卷 / 11期
关键词：
D O I：
10.1182/blood.V106.11.2235.2235
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
2235
引用
收藏
页码：629A / 630A
页数：2
相关论文
共 50 条
  • [21] Changes in the atherogenic profile of patients with type 1 Gaucher disease after miglustat therapy
    Puzo, J.
    Alfonso, P.
    Irun, P.
    Gervas, J.
    Pocovi, M.
    Giraldo, P.
    ATHEROSCLEROSIS, 2010, 209 (02) : 515 - 519
  • [22] Gaucher disease linked to a deficit in saposine C with treatment by miglustat
    Amsallem, Daniel
    PRESSE MEDICALE, 2006, 35 : S35 - S36
  • [23] A TREATMENT EXPERIENCE OF TYPE 3 GAUCHER DISEASE: PIRACETAM AND MIGLUSTAT THERAPY IN PROGRESSIVE MYOCLONIC EPILEPSY
    Onal, H.
    Adal, E.
    Ersen, A.
    Aydin, A.
    JOURNAL OF INHERITED METABOLIC DISEASE, 2010, 33 : S151 - S151
  • [24] EFFECTIVE SHORT-TERM TREATMENT OF PAGETS-DISEASE WITH ORAL ETIDRONATE
    PRESTON, CJ
    YATES, AJP
    BENETON, MNC
    RUSSELL, RGG
    GRAY, RES
    SMITH, R
    KANIS, JA
    BRITISH MEDICAL JOURNAL, 1986, 292 (6513): : 79 - 80
  • [25] Effect of enzyme replacement therapy on bone mineral density in type 1 Gaucher disease.
    Wenstrup, R
    Kacena, K
    Kaplan, P
    Pastores, G
    Prakash-Cheng, A
    Zimran, A
    Hangartner, T
    BLOOD, 2005, 106 (11) : 54B - 54B
  • [26] Short-term efficacy of donepezil in Alzheimer's disease.
    McMillan, J
    ARCHIVES OF CLINICAL NEUROPSYCHOLOGY, 1999, 14 (08) : 629 - 630
  • [27] Treat type I Gaucher disease with miglustat - Experience with two patients
    Yang, Sandra
    Tifft, Cynthia
    MOLECULAR GENETICS AND METABOLISM, 2007, 92 (04) : S22 - S22
  • [28] Randomized, Controlled Trial of Miglustat in Gaucher's Disease Type 3
    Schiffmann, Raphael
    Fitzgibbon, Edmond J.
    Harris, Chris
    DeVile, Catherine
    Davies, Elin H.
    Abel, Larry
    van Schaik, Ivo N.
    Benko, William
    Timmons, Margaret
    Ries, Markus
    Vellodi, Ashok
    ANNALS OF NEUROLOGY, 2008, 64 (05) : 514 - 522
  • [29] Hepcidin dysregulation in patients with type 1 Gaucher's disease.
    Hughes, DA
    Li, A
    Keshav, S
    Mehta, A
    BLOOD, 2004, 104 (11) : 42B - 43B
  • [30] Encore! Oral therapy for type 1 Gaucher disease
    Weinreb, Neal J.
    BLOOD, 2017, 129 (17) : 2337 - 2338
12345